4 studies found for:    18441371 [PUBMED-IDS]
Show Display Options
Rank Status Study
1 Active, not recruiting An Open Label Clinical Trial of Retinal Gene Therapy for Choroideremia
Condition: Choroideremia
Intervention: Genetic: rAAV2.REP1 vector
2 Completed
Has Results
Safety and Efficacy Study of rAAV2-ND4 Treatment of Leber Hereditary Optic Neuropathy (LHON)
Condition: Leber Hereditary Optic Neuropathy
Intervention: Drug: rAAV2-ND4
3 Recruiting Clinical Trial of Gene Therapy for Leber Congenital Amaurosis Caused by RPE65 Mutations
Condition: Leber Congenital Amaurosis
Intervention: Genetic: rAAV2-hRPE65
4 Completed Safety Study of RPE65 Gene Therapy to Treat Leber Congenital Amaurosis
Condition: Retinal Degeneration
Intervention: Biological: tgAAG76 (rAAV 2/2.hRPE65p.hRPE65)

Indicates status has not been verified in more than two years