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2 studies found for:    22149959 [PUBMED-IDS]
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Rank Status Study
1 Recruiting Dose-Escalation Study Of A Self Complementary Adeno-Associated Viral Vector For Gene Transfer in Hemophilia B
Condition: Hemophilia B
Interventions: Genetic: Gene Transfer;   Drug: scAAV2/8-LP1-hFIXco
2 Recruiting A Gene Therapy Study for Homozygous Familial Hypercholesterolemia (HoFH)
Condition: Homozygous Familial Hypercholesterolemia
Intervention: Biological: AAV directed hLDLR gene therapy

Study has passed its completion date and status has not been verified in more than two years.