Study record managers: refer to the Data Element Definitions if submitting registration or results information.
|1||NCT02852213||Recruiting||A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric Patients||
||Other / NIH||
||6||All||5 Years to 18 Years (Child, Adult)||NCT02852213||15-17756
|AADC||July 2016||December 2020||June 2021||August 2, 2016||November 28, 2018||