Gene Therapy for ADA-SCID
|2||Active, not recruiting||
ADA Gene Transfer Into Hematopoietic Stem/Progenitor Cells for the Treatment of ADA-SCID
|3||Active, not recruiting||
Gene Therapy for Wiskott-Aldrich Syndrome
Gene Therapy for Transfusion Dependent Beta-thalassemia
† Study has passed its completion date and status has not been verified in more than two years.