6 studies found for: Open Studies | "Tay-Sachs Disease"
Biomarker for GM1/GM2 - Gangliosidoses
A Natural History Study of the Gangliosidoses
Synergistic Enteral Regimen for Treatment of the Gangliosidoses
Efficacy Study of an Online Educational Module Before Carrier Genetic Screening in Persons of Ashkenazi Jewish Descent.
HSCT for High Risk Inherited Inborn Errors
UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
† Indicates status has not been verified in more than two years