8 studies found for: Open Studies | "Leukodystrophy, Metachromatic"
Intracerebral Gene Therapy for Children With Early Onset Forms of Metachromatic Leukodystrophy
Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy
Biomarker for Metachromatic Leukodystrophy Disease
|4||Not yet recruiting||
Safety and Exploratory Efficacy of HSC835 in Patients With Inherited Metabolic Disorders (IMD)
UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
Human Placental-Derived Stem Cell Transplantation
MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
Reduced Intensity Conditioning in Patients Aged ≤35 With Non-Malignant Disorders Undergoing UCBT, BMT, or PBSCT
† Study has passed its completion date and status has not been verified in more than two years.