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A Dose-escalation and Safety & Efficacy Study of AXO-AAV-GM2 in Tay-Sachs or Sandhoff Disease

The safety and scientific validity of this study is the responsibility of the study sponsor and investigators. Listing a study does not mean it has been evaluated by the U.S. Federal Government. Know the risks and potential benefits of clinical studies and talk to your health care provider before participating. Read our disclaimer for details. Identifier: NCT04669535
Recruitment Status : Recruiting
First Posted : December 17, 2020
Last Update Posted : January 29, 2021
University of Massachusetts, Worcester
Massachusetts General Hospital
Information provided by (Responsible Party):
Sio Gene Therapies

No Study Results Posted on for this Study
Recruitment Status : Recruiting
Estimated Primary Completion Date : November 2024
Estimated Study Completion Date : June 2028