Working…
ClinicalTrials.gov
ClinicalTrials.gov Menu

Single-Dose Gene Replacement Therapy Using for Patients With Spinal Muscular Atrophy Type 1 With One or Two SMN2 Copies

The safety and scientific validity of this study is the responsibility of the study sponsor and investigators. Listing a study does not mean it has been evaluated by the U.S. Federal Government. Know the risks and potential benefits of clinical studies and talk to your health care provider before participating. Read our disclaimer for details.
 
ClinicalTrials.gov Identifier: NCT03837184
Recruitment Status : Recruiting
First Posted : February 12, 2019
Last Update Posted : August 14, 2019
Sponsor:
Collaborator:
PRA Health Sciences
Information provided by (Responsible Party):
AveXis, Inc.

No Study Results Posted on ClinicalTrials.gov for this Study
Recruitment Status : Recruiting
Estimated Primary Completion Date : April 1, 2021
Estimated Study Completion Date : April 1, 2021