Try our beta test site
IMPORTANT: Listing of a study on this site does not reflect endorsement by the National Institutes of Health. Talk with a trusted healthcare professional before volunteering for a study. Read more...

Phase I/II Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH for Mucopolysaccharidosis (MPS) IIIA

This study is currently recruiting participants. (see Contacts and Locations)
Verified February 2017 by Nationwide Children's Hospital
Sponsor:
Collaborator:
Abeona Therapeutics
Information provided by (Responsible Party):
Kevin Flanigan, Nationwide Children's Hospital
ClinicalTrials.gov Identifier:
NCT02716246
First received: March 17, 2016
Last updated: February 6, 2017
Last verified: February 2017
No Study Results Posted on ClinicalTrials.gov for this Study
  Study Status: This study is currently recruiting participants.
  Estimated Study Completion Date: December 2020
  Estimated Primary Completion Date: December 2019 (Final data collection date for primary outcome measure)