Safety and Efficacy Study in Subjects With Leber Congenital Amaurosis
This study is ongoing, but not recruiting participants.
Children's Hospital of Philadelphia
University of Iowa
Information provided by (Responsible Party):
First received: October 21, 2009
Last updated: July 22, 2016
Last verified: July 2016
No Study Results Posted on ClinicalTrials.gov for this Study
|Study Status:||This study is ongoing, but not recruiting participants.|
|Estimated Study Completion Date:||July 2029|
|Primary Completion Date:||July 2015 (Final data collection date for primary outcome measure)|
|Certification or Request for Extension to Delay Results Received:||February 16, 2016|
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Simonelli F, Maguire AM, Testa F, Pierce EA, Mingozzi F, Bennicelli JL, Rossi S, Marshall K, Banfi S, Surace EM, Sun J, Redmond TM, Zhu X, Shindler KS, Ying GS, Ziviello C, Acerra C, Wright JF, McDonnell JW, High KA, Bennett J, Auricchio A. Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration. Mol Ther. 2010 Mar;18(3):643-50. doi: 10.1038/mt.2009.277.
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