Safety and Efficacy Study in Subjects With Leber Congenital Amaurosis

The safety and scientific validity of this study is the responsibility of the study sponsor and investigators. Listing a study does not mean it has been evaluated by the U.S. Federal Government. Read our disclaimer for details. Identifier: NCT00999609
Recruitment Status : Active, not recruiting
First Posted : October 22, 2009
Last Update Posted : March 28, 2017
Children's Hospital of Philadelphia
University of Iowa
Information provided by (Responsible Party):
Spark Therapeutics

Results Submitted - Not Posted on
Results information has been submitted to by the sponsor or investigator, but is not yet publicly available (or "posted") on The submitted information may not be available if it is pending Quality Control (QC) Review by the National Library of Medicine (NLM) or if issues identified during QC review are being addressed or corrected by the sponsor or investigator. NLM's limited QC review assesses for apparent errors, deficiencies, or inconsistencies. NLM staff do not verify the scientific validity or relevance of the submitted information.
  Recruitment Status : Active, not recruiting
  Primary Completion Date : July 2015
  Estimated Study Completion Date : July 2029
  Certification/Extension First Submitted : February 16, 2016

Submission Cycle Results Submitted to Results Returned after Quality Control Review
1 January 12, 2018 February 7, 2018
2 February 23, 2018  
Publications of Results:
Other Publications:
Publications automatically indexed to this study by Identifier (NCT Number):