A Study of Intrathecal Enzyme Therapy for Cognitive Decline in MPS I

This study is currently recruiting participants. (see Contacts and Locations)
Verified June 2013 by Dickson, Patricia I., M.D.
MPS I Intrathecal Research Collaborative
The Ryan Foundation
BioMarin Pharmaceutical
Rare Diseases Clinical Research Network
University of Minnesota - Clinical and Translational Science Institute
University of California, Los Angeles
Information provided by (Responsible Party):
Patricia I. Dickson, M.D., Dickson, Patricia I., M.D.
ClinicalTrials.gov Identifier:
First received: February 25, 2009
Last updated: June 18, 2013
Last verified: June 2013
No Study Results Posted on ClinicalTrials.gov for this Study
  Study Status: This study is currently recruiting participants.
  Estimated Study Completion Date: December 2018
  Estimated Primary Completion Date: December 2014 (Final data collection date for primary outcome measure)