A Study of Intrathecal Enzyme Therapy for Cognitive Decline in MPS I

This study is currently recruiting participants. (see Contacts and Locations)
Verified June 2013 by Dickson, Patricia I., M.D.
MPS I Intrathecal Research Collaborative
The Ryan Foundation
BioMarin Pharmaceutical
Rare Diseases Clinical Research Network
National Center for Advancing Translational Science (NCATS)
National Institute of Neurological Disorders and Stroke (NINDS)
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
University of Minnesota - Clinical and Translational Science Institute
University of California, Los Angeles
Information provided by (Responsible Party):
Patricia I. Dickson, M.D., Dickson, Patricia I., M.D.
ClinicalTrials.gov Identifier:
First received: February 25, 2009
Last updated: June 18, 2013
Last verified: June 2013
No Study Results Posted on ClinicalTrials.gov for this Study
  Study Status: This study is currently recruiting participants.
  Estimated Study Completion Date: December 2018
  Estimated Primary Completion Date: December 2014 (Final data collection date for primary outcome measure)