Trial record 5 of 7 for:
Recruiting, Not yet recruiting, Available Studies | "Tay-Sachs Disease"
Longitudinal Study of Neurodegenerative Disorders
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ClinicalTrials.gov Identifier: NCT03333200 |
Recruitment Status
:
Recruiting
First Posted
: November 6, 2017
Last Update Posted
: February 1, 2018
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Sponsor:
University of Pittsburgh
Information provided by (Responsible Party):
Maria Escolar, University of Pittsburgh
Tracking Information | |||||||||
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First Submitted Date | April 24, 2017 | ||||||||
First Posted Date | November 6, 2017 | ||||||||
Last Update Posted Date | February 1, 2018 | ||||||||
Actual Study Start Date | January 11, 2012 | ||||||||
Estimated Primary Completion Date | January 2030 (Final data collection date for primary outcome measure) | ||||||||
Current Primary Outcome Measures |
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Original Primary Outcome Measures | Same as current | ||||||||
Change History | Complete list of historical versions of study NCT03333200 on ClinicalTrials.gov Archive Site | ||||||||
Current Secondary Outcome Measures |
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Original Secondary Outcome Measures | Same as current | ||||||||
Current Other Outcome Measures | Not Provided | ||||||||
Original Other Outcome Measures | Not Provided | ||||||||
Descriptive Information | |||||||||
Brief Title | Longitudinal Study of Neurodegenerative Disorders | ||||||||
Official Title | Longitudinal Study of Neurodegenerative Disorders | ||||||||
Brief Summary | The purpose of this study is to understand the course of rare genetic disorders that affect the brain. This data is being analyzed to gain a better understanding of the progression of the rare neurodegenerative disorders and the effects of interventions. | ||||||||
Detailed Description | Patients would be evaluated by a multidisciplinary team at specific time points every 3 months the first year, every 6 months the second year and once a year thereafter. | ||||||||
Study Type | Observational | ||||||||
Study Design | Observational Model: Cohort Time Perspective: Prospective |
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Target Follow-Up Duration | Not Provided | ||||||||
Biospecimen | Retention: Samples With DNA Description: NDRD Biorepository includes: blood plasma and serum, CSF, brain and other tissues |
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Sampling Method | Non-Probability Sample | ||||||||
Study Population | Persons with genetic neurodegenerative diseases. | ||||||||
Condition |
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Intervention |
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Study Groups/Cohorts | Not Provided | ||||||||
Publications * | Not Provided | ||||||||
* Includes publications given by the data provider as well as publications identified by ClinicalTrials.gov Identifier (NCT Number) in Medline. |
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Recruitment Information | |||||||||
Recruitment Status | Recruiting | ||||||||
Estimated Enrollment |
1500 | ||||||||
Original Estimated Enrollment | Same as current | ||||||||
Estimated Study Completion Date | January 2035 | ||||||||
Estimated Primary Completion Date | January 2030 (Final data collection date for primary outcome measure) | ||||||||
Eligibility Criteria | Inclusion Criteria:
Exclusion Criteria: |
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Sex/Gender |
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Ages | Child, Adult, Senior | ||||||||
Accepts Healthy Volunteers | No | ||||||||
Contacts |
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Listed Location Countries | United States | ||||||||
Removed Location Countries | |||||||||
Administrative Information | |||||||||
NCT Number | NCT03333200 | ||||||||
Other Study ID Numbers | PRO11050036 | ||||||||
Has Data Monitoring Committee | No | ||||||||
U.S. FDA-regulated Product |
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IPD Sharing Statement |
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Responsible Party | Maria Escolar, University of Pittsburgh | ||||||||
Study Sponsor | University of Pittsburgh | ||||||||
Collaborators | Not Provided | ||||||||
Investigators | Not Provided | ||||||||
PRS Account | University of Pittsburgh | ||||||||
Verification Date | January 2018 |