Muscle Response to Enzyme Replacement Therapy in Pompe Disease

This study is currently recruiting participants. (see Contacts and Locations)
Verified March 2015 by National Taiwan University Hospital
Sponsor:
Information provided by (Responsible Party):
National Taiwan University Hospital
ClinicalTrials.gov Identifier:
NCT00713453
First received: July 9, 2008
Last updated: March 21, 2015
Last verified: March 2015

July 9, 2008
March 21, 2015
January 2007
December 2019   (final data collection date for primary outcome measure)
all morphology changes improvement [ Time Frame: 6 months ] [ Designated as safety issue: Yes ]
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Complete list of historical versions of study NCT00713453 on ClinicalTrials.gov Archive Site
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Muscle Response to Enzyme Replacement Therapy in Pompe Disease
Muscle Response to Enzyme Replacement Therapy in Pompe Disease
This study is to study the response of muscle cells from Pompe disease after enzyme replacement therapy
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Observational
Observational Model: Case-Only
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Non-Probability Sample
patients with Pompe disease, prepare or on enzyme replacement therapy
Pompe Disease
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*   Includes publications given by the data provider as well as publications identified by ClinicalTrials.gov Identifier (NCT Number) in Medline.
 
Recruiting
16
December 2019
December 2019   (final data collection date for primary outcome measure)

Inclusion Criteria:

  • patients with Pompe disease, prepare or on enzyme replacement therapy
  • signed informed consent

Exclusion Criteria:

Both
Child, Adult, Senior
Yes
Contact: Yin-Hsiu Chien, MD 886-2-23123456 ext 71937 chienyh@ntu.edu.tw
Taiwan
 
NCT00713453
200704066R
No
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National Taiwan University Hospital
National Taiwan University Hospital
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Principal Investigator: Yin-Hsiu Chien, MD National Taiwan University Hospital
National Taiwan University Hospital
March 2015

ICMJE     Data element required by the International Committee of Medical Journal Editors and the World Health Organization ICTRP