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Muscle Response to Enzyme Replacement Therapy in Pompe Disease

This study is currently recruiting participants.
Verified March 2015 by National Taiwan University Hospital
Sponsor:
ClinicalTrials.gov Identifier:
NCT00713453
First Posted: July 11, 2008
Last Update Posted: March 24, 2015
The safety and scientific validity of this study is the responsibility of the study sponsor and investigators. Listing a study does not mean it has been evaluated by the U.S. Federal Government. Know the risks and potential benefits of clinical studies and talk to your health care provider before participating. Read our disclaimer for details.
Information provided by (Responsible Party):
National Taiwan University Hospital
July 9, 2008
July 11, 2008
March 24, 2015
January 2007
December 2019   (Final data collection date for primary outcome measure)
all morphology changes improvement [ Time Frame: 6 months ]
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Complete list of historical versions of study NCT00713453 on ClinicalTrials.gov Archive Site
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Muscle Response to Enzyme Replacement Therapy in Pompe Disease
Muscle Response to Enzyme Replacement Therapy in Pompe Disease
This study is to study the response of muscle cells from Pompe disease after enzyme replacement therapy
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Observational
Observational Model: Case-Only
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Non-Probability Sample
patients with Pompe disease, prepare or on enzyme replacement therapy
Pompe Disease
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*   Includes publications given by the data provider as well as publications identified by ClinicalTrials.gov Identifier (NCT Number) in Medline.
 
Recruiting
16
December 2019
December 2019   (Final data collection date for primary outcome measure)

Inclusion Criteria:

  • patients with Pompe disease, prepare or on enzyme replacement therapy
  • signed informed consent

Exclusion Criteria:

Sexes Eligible for Study: All
Child, Adult, Senior
Yes
Contact: Yin-Hsiu Chien, MD 886-2-23123456 ext 71937 chienyh@ntu.edu.tw
Taiwan
 
 
NCT00713453
200704066R
No
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National Taiwan University Hospital
National Taiwan University Hospital
Not Provided
Principal Investigator: Yin-Hsiu Chien, MD National Taiwan University Hospital
National Taiwan University Hospital
March 2015