Observational Study Investigating Clinical & Anthropometric Characteristics of Children With Achondroplasia.
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|ClinicalTrials.gov Identifier: NCT03794609|
Recruitment Status : Recruiting
First Posted : January 7, 2019
Last Update Posted : June 15, 2021
This is a registry study in children with achondroplasia, age 0-10 years, to be conducted at multiple clinical centers in several countries. Information collected will include in anthropometric characteristics, related symptoms, tests, & treatments
Children's information will be collected in the registry for a maximum of 5 years.
|Condition or disease|
|Study Type :||Observational|
|Estimated Enrollment :||200 participants|
|Official Title:||A Multi-center, Prospective, Longitudinal, Observational Study to Investigate the Clinical and Anthropometric Characteristics of Children With the Diagnosis Achondroplasia.|
|Actual Study Start Date :||June 15, 2018|
|Estimated Primary Completion Date :||September 5, 2028|
|Estimated Study Completion Date :||September 6, 2028|
- Collection of Natural History of Achondroplasia Characteristics in a cohort of Children aged 0-10 years old diagnosed with Achondroplasia [ Time Frame: Up to 5 Years ]To quantify the number & type of Achondroplasia Characteristics by review of medical records
- Collection of Natural History of Achondroplasia Symptoms in a cohort of Children aged 0-10 years old diagnosed with Achondroplasia [ Time Frame: Up to 5 Years ]To quantify the number & type of Achondroplasia Symptoms by review of medical records
- Collection of Natural History of Achondroplasia related Tests & Treatments in a cohort of Children aged 0-10 years old diagnosed with Achondroplasia [ Time Frame: Up to 5 Years ]To quantify the number & type of Achondroplasia related Tests & Treatments by review of medical records
- Measurement of biomarkers for bone growth [ Time Frame: Baseline, Month 12, Month 24, Month 36, Month 48, Month 60 ]changes from Baseline in blood samples of collagen fragments
To learn more about this study, you or your doctor may contact the study research staff using the contact information provided by the sponsor.
Please refer to this study by its ClinicalTrials.gov identifier (NCT number): NCT03794609
|Contact: Pfizer CT.gov Call Center||1-800-718-1021||ClinicalTrials.gov_Inquiries@pfizer.com|
|Study Director:||Pfizer CT.gov Call Center||Pfizer|