Observational Study Investigating Clinical & Anthropometric Characteristics of Children With Achondroplasia.
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|ClinicalTrials.gov Identifier: NCT03794609|
Recruitment Status : Active, not recruiting
First Posted : January 7, 2019
Last Update Posted : November 18, 2022
This is a registry study in children with achondroplasia, age 0-10 years, to be conducted at multiple clinical centers in several countries. Information collected will include in anthropometric characteristics, related symptoms, tests, & treatments
Children's information will be collected in the registry for a maximum of 5 years.
|Condition or disease|
|Study Type :||Observational|
|Actual Enrollment :||315 participants|
|Official Title:||An International, Prospective Registry Investigating the Natural History of Participants With Achondroplasia|
|Actual Study Start Date :||June 15, 2018|
|Estimated Primary Completion Date :||September 29, 2027|
|Estimated Study Completion Date :||September 29, 2027|
- Collection of Natural History of Achondroplasia Characteristics in a cohort of Children aged 0-10 years old diagnosed with Achondroplasia [ Time Frame: Up to 5 Years ]To quantify the number & type of Achondroplasia Characteristics by review of medical records
- Collection of Natural History of Achondroplasia Symptoms in a cohort of Children aged 0-10 years old diagnosed with Achondroplasia [ Time Frame: Up to 5 Years ]To quantify the number & type of Achondroplasia Symptoms by review of medical records
- Collection of Natural History of Achondroplasia related Tests & Treatments in a cohort of Children aged 0-10 years old diagnosed with Achondroplasia [ Time Frame: Up to 5 Years ]To quantify the number & type of Achondroplasia related Tests & Treatments by review of medical records
- Measurement of biomarkers for bone growth [ Time Frame: Baseline, Month 12, Month 24, Month 36, Month 48, Month 60 ]changes from Baseline in blood samples of collagen fragments
To learn more about this study, you or your doctor may contact the study research staff using the contact information provided by the sponsor.
Please refer to this study by its ClinicalTrials.gov identifier (NCT number): NCT03794609
|Study Director:||Pfizer Pfizer CT.gov Call Center||Pfizer|