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CRD007 for the Treatment of Duchenne Muscular Dystrophy, Becker Muscular Dystrophy and Symptomatic Carriers

This study has been completed.
Information provided by (Responsible Party):
RSPR Pharma AB Identifier:
First received: February 23, 2012
Last updated: October 1, 2012
Last verified: October 2012
This is an investigation of the efficacy and safety of CRD007 in Duchenne Muscular Dystrophy (DMD), Becker Muscular Dystrophy (BMD) and symptomatic carriers.

Condition Intervention Phase
Duchenne Muscular Dystrophy
Becker Muscular Dystrophy
Drug: CRD007
Phase 2

Study Type: Interventional
Official Title: An Open-label, Un-controlled, Single-centre Trial Investigating the Efficacy and Safety of CRD007 in Children With Duchenne Muscular Dystrophy (DMD) or Becker Muscular Dystrophy (BMD) or Children Being Symptomatic Carriers for DMD or BMD

Resource links provided by NLM:

Further study details as provided by RSPR Pharma AB:

Arms Assigned Interventions
Experimental: CRD007 10 mg tablet Drug: CRD007


Ages Eligible for Study:   2 Years to 11 Years   (Child)
Sexes Eligible for Study:   All

Inclusion Criteria:

  • Documented diagnosis of dystrophinopathy

Exclusion Criteria:

  • Severe functional impairment
  Contacts and Locations
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Please refer to this study by its identifier: NCT01540604

Stockholm, Sweden
Sponsors and Collaborators
RSPR Pharma AB
Principal Investigator: T Sejersen, MD PhD Karolinska University Hospital
  More Information

Responsible Party: RSPR Pharma AB Identifier: NCT01540604     History of Changes
Other Study ID Numbers: Cardoz-004
Study First Received: February 23, 2012
Last Updated: October 1, 2012

Keywords provided by RSPR Pharma AB:
symptomatic carriers

Additional relevant MeSH terms:
Muscular Dystrophies
Muscular Dystrophy, Duchenne
Muscular Disorders, Atrophic
Muscular Diseases
Musculoskeletal Diseases
Neuromuscular Diseases
Nervous System Diseases
Genetic Diseases, Inborn
Genetic Diseases, X-Linked processed this record on May 25, 2017