This is a Study to Get More Information About Non Ambulatory Boys & Men With Duchenne Muscular Dystrophy (DMD)
|The safety and scientific validity of this study is the responsibility of the study sponsor and investigators. Listing a study does not mean it has been evaluated by the U.S. Federal Government. Read our disclaimer for details.|
|ClinicalTrials.gov Identifier: NCT01098708|
Recruitment Status : Completed
First Posted : April 5, 2010
Last Update Posted : January 18, 2017
|Condition or disease|
|Duchenne Muscular Dystrophy|
For Non-ambulatory study, boys must be unable to walk without assistive devices for greater than or equal to one year.
Age at onset of study for non-ambulatory boys and men: greater than or equal to 7 years through age 22 years.
Genetic or biopsy confirmation of dystrophinopathy or clinical diagnosis of DMD with biopsy/genetic confirmation in a primary relative.
|Study Type :||Observational|
|Actual Enrollment :||50 participants|
|Official Title:||Clinical Outcomes Validation in Non Ambulatory and Young Boys/Men With Duchenne Muscular Dystrophy (DMD)|
|Study Start Date :||March 2010|
|Actual Primary Completion Date :||November 2013|
|Actual Study Completion Date :||November 2013|
- Dystrophin gene mutations that predispose to early onset cardiomyopathy [ Time Frame: 3 years ]
To learn more about this study, you or your doctor may contact the study research staff using the contact information provided by the sponsor.
Please refer to this study by its ClinicalTrials.gov identifier (NCT number): NCT01098708
|United States, Missouri|
|St. Louis, Missouri, United States, 63110|
|Principal Investigator:||Anne Connolly, M.D.||Washington University School of Medicine|