|1||Active, not recruiting||
A Study to Assess the Efficacy, Safety and Pharmacokinetics of IONIS SMNRx in Infants With Spinal Muscular Atrophy
|2||Enrolling by invitation||
A Study for Participants With Spinal Muscular Atrophy (SMA) Who Previously Participated in Nusinersen (ISIS 396443) Investigational Studies.
† Study has passed its completion date and status has not been verified in more than two years.