103 studies found for:    GBA
Show Display Options
Rank Status Study
21 Completed Safety and Efficacy of ISU302 in Patients With Type 1 Gaucher Disease
Condition: Gaucher Disease, Type 1
Intervention: Drug: ISU302
22 Unknown  Thrombocytopathy in Gaucher Disease Patients
Conditions: Gaucher Disease;   Thrombocytopathy
Intervention:
23 Unknown  The Safety and Efficacy Study of ISU302 in Patient With Type I Gaucher Disease
Condition: Gaucher Disease
Interventions: Drug: Cerezyme®;   Drug: ISU302
24 Completed
Has Results
Plant Cell Expressed Recombinant Human Glucocerebrosidase Extension Trial
Condition: Gaucher Disease
Intervention: Drug: Taliglucerase alfa
25 Completed
Has Results
A Multicenter Extension Study of Taliglucerase Alfa in Pediatric Subjects With Gaucher Disease
Condition: Gaucher Disease
Intervention: Drug: Taliglucerase alfa
26 Completed
Has Results
A Safety and Efficacy Study of Two Dose Levels of Taliglucerase Alfa in Pediatric Subjects With Gaucher Disease
Condition: Gaucher Disease
Intervention: Drug: Taliglucerase alfa
27 Recruiting Biomarker for Gaucher Disease
Conditions: Lysosomal Storage Diseases;   Gaucher Disease;   Sphingolipidoses
Intervention:
28 Completed
Has Results
A Phase III Trial to Assess the Safety and Efficacy of Plant Cell Expressed GCD in Patients With Gaucher Disease
Condition: Gaucher Disease
Intervention: Drug: Plant cell expressed recombinant glucocerebrosidase (prGCD)
29 Completed Study to Evaluate Blood Cell Lines From Patients With Gaucher Disease
Condition: Gaucher Disease
Intervention: Procedure: Blood sample
30 Active, not recruiting Exploration of Immunity in Gaucher Disease
Condition: Gaucher Disease
Intervention:
31 Recruiting Oxidative Stress-Related Biomarkers in Gaucher Disease: A Preliminary Study
Conditions: Gaucher Disease Type I;   Oxidative Stress
Intervention:
32 Enrolling by invitation Identification of Undiagnosed Gaucher Disease
Condition: Gaucher Disease
Intervention: Other: Enzyme analysis
33 Completed PEG-Glucocerebrosidase for the Treatment of Gaucher Disease
Condition: Gaucher's Disease
Intervention: Drug: Lysodase
34 Completed Convection-Enhanced Delivery of Glucocerebrosidase to Treat Type 2 Gaucher Disease
Condition: Type 2 Gaucher Disease
Intervention:
35 Suspended Clinical Trial of Ambroxol in Patients With Type I Gaucher Disease
Condition: Type I Gaucher Disease
Intervention: Drug: Ambroxol
36 Completed Effects of Enzyme Replacement in Gaucher's Disease
Condition: Gaucher's Disease
Intervention:
37 Completed Phase I Single Dose-Escalation Safety Study of Human Glucocerebrosidase (prGCD)
Condition: Gaucher Disease
Intervention: Drug: Human Glucocerebrosidase (prGCD)
38 Completed
Has Results
Auto-antibodies Prevalence and CD1 Role in Gaucher Disease
Condition: Gaucher Disease
Intervention: Genetic: genetic analyses
39 Completed
Has Results
Study of Velaglucerase Alfa Enzyme Replacement Therapy in Japanese Patients With Gaucher Disease
Condition: Gaucher Disease
Intervention: Biological: velaglucerase alfa
40 Completed
Has Results
Efficacy and Safety Study of Velaglucerase Alfa in Children and Adolescents With Type 3 Gaucher Disease
Condition: Gaucher Disease, Type 3
Intervention: Biological: velaglucerase alfa

First Page    Show previous page of results Previous Page (1-20) Studies Shown (21-40) Next Page (41-60) Show next page of results    Last Page
Indicates status has not been verified in more than two years