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718 studies found for:    DMD
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Rank Status Study
21 Completed A Clinical Study to Assess the Efficacy and Safety of GSK2402968 in Subjects With Duchenne Muscular Dystrophy
Condition: Muscular Dystrophies
Intervention: Drug: GSK2402968 6mg/kg/week
22 Recruiting Validating Cardiac MRI Biomarkers and Genotype-Phenotype Correlations for DMD
Condition: Muscular Dystrophy, Duchenne
Interventions: Other: Cardiac MRI with contrast;   Other: Cardiac MRI without contrast;   Other: Blood Test;   Other: Heart Rate;   Other: Pulmonary Function Test;   Other: Genetic Testing;   Other: Repeat MRI scan
23 Active, not recruiting Allogeneic Human Umbilical Cord Mesenchymal Stem Cells for a Single Male Patient With Duchenne Muscular Dystrophy (DMD)
Condition: Duchenne's Muscular Dystrophy
Intervention: Biological: Umbilical Cord Mesenchymal Stem Cells
24 Active, not recruiting Efficacy, Safety, and Tolerability Rollover Study of Eteplirsen in Subjects With Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy (DMD)
Intervention: Drug: AVI-4658 (Eteplirsen)
25 Active, not recruiting Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Biological: rAAVrh74.MCK.micro-Dystrophin
26 Terminated Safety, Tolerability, and Pharmacokinetics of Single and Multiple Doses of HT-100 in Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Drug: HT-100
27 Unknown  Endomysial Fibrosis, Muscular Inflammatory Response and Calcium Homeostasis Dysfunction in Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Distrophy (DMD)
Intervention: Other: Muscle biopsy
28 Active, not recruiting Phase I/II Study of SRP-4053 in DMD Patients
Condition: Duchenne Muscular Dystrophy
Interventions: Drug: Placebo;   Drug: SRP-4053
29 Recruiting A Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)
Condition: Duchenne Muscular Dystrophy
Interventions: Drug: Vamorolone 0.25 mg/kg/day;   Drug: Vamorolone 0.75 mg/kg/day;   Drug: Vamorolone 2.0 mg/kg/day;   Drug: Vamorolone 6.0 mg/kg/day
30 Completed Safety and Efficacy Study of PTC124 in Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Drug: PTC124
31 Completed Phase 3 Study of Ataluren in Patients With Nonsense Mutation Duchenne Muscular Dystrophy
Conditions: Muscular Dystrophy, Duchenne;   Muscular Dystrophies;   Muscular Disorders, Atrophic;   Muscular Diseases;   Musculoskeletal Diseases;   Neuromuscular Diseases;   Nervous System Diseases;   Genetic Diseases, X-Linked;   Genetic Diseases, Inborn
Interventions: Drug: Ataluren;   Drug: Placebo
32 Completed L-citrulline and Metformin in Duchenne's Muscular Dystrophy
Condition: Duchenne's Muscular Dystrophy (DMD)
Interventions: Drug: 750 mg metformin and 7.5 g L-citrulline daily p.o.;   Drug: Placebo
33 Recruiting An Extension Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)
Condition: Duchenne Muscular Dystrophy
Interventions: Drug: Vamorolone 0.25 mg/day/day;   Drug: Vamorolone 0.75 mg/day/day;   Drug: Vamorolone 2.0 mg/day/day;   Drug: Vamorolone 6.0 mg/day/day
34 Enrolling by invitation Long-term Extension Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)
Condition: Duchenne Muscular Dystrophy
Interventions: Drug: Vamorolone 0.25 mg/day/day;   Drug: Vamorolone 0.75 mg/day/day;   Drug: Vamorolone 2.0 mg/day/day;   Drug: Vamorolone 6.0 mg/day/day
35 Recruiting Safety Study of Eteplirsen to Treat Early Stage Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy (DMD)
Intervention: Drug: eteplirsen
36 Terminated Phase 2a Extension Study of Ataluren (PTC124) in Duchenne Muscular Dystrophy (DMD)
Condition: Duchenne Muscular Dystrophy
Intervention: Drug: Ataluren
37 Completed Research of Biomarkers in Duchenne Muscular Dystrophy Patients
Condition: Duchenne Muscular Dystrophy (DMD)
Intervention:
38 Completed
Has Results
Efficacy Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy Patients
Condition: Duchenne Muscular Dystrophy
Interventions: Drug: AVI-4658 (Eteplirsen);   Other: Placebo
39 Withdrawn Drisapersen Duchenne Muscular Dystrophy (DMD) Treatment Protocol
Condition: Muscular Dystrophies
Intervention: Drug: Drisapersen
40 Active, not recruiting Clinical Intramuscular Gene Transfer of rAAV1.CMV.huFollistatin344 Trial to Patients With Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Biological: rAAV1.CMV.huFollistin344

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Study has passed its completion date and status has not been verified in more than two years.