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3 studies found for:    ALXN1101
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Rank Status Study
1 Completed Phase 1 Single Dose Study of ALXN1101 in Healthy Volunteers
Conditions: Molybdenum Cofactor Deficiency (MoCD);   Rare Autosomal Recessive Disorder;   Deficiency of Activity of Molybdenum-dependent Enzymes (Sulfite Oxidase [SOX], Xanthine Dehydrogenase, and Aldehyde Oxidase)
Interventions: Drug: ALXN1101;   Drug: Placebo
2 Active, not recruiting Safety & Efficacy Study of ALXN1101 in Pediatric Patients With MoCD Type A Currently Treated With rcPMP
Condition: Molybdenum Cofactor Deficiency, Type A
Intervention: Drug: ALXN1101
3 Recruiting Study of ALXN1101 in Neonates With Molybdenum Cofactor Deficiency (MOCD) Type A
Condition: Molybdenum Cofactor Deficiency, Type A
Intervention: Drug: ALXN1101

Study has passed its completion date and status has not been verified in more than two years.