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1 study found for:    "spinal muscular atrophy" AND AAV
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Rank Status Study
1 Active, not recruiting Gene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1
Condition: Spinal Muscular Atrophy 1
Intervention: Biological: AVXS-101

Study has passed its completion date and status has not been verified in more than two years.