|1||NCT03179631||Recruiting||Long-Term Outcomes of Ataluren in Duchenne Muscular Dystrophy||
||250||Male||5 Years and older (Child, Adult, Older Adult)||NCT03179631||PTC124-GD-041-DMD||July 6, 2017||March 31, 2020||December 31, 2021||June 7, 2017||October 25, 2018||
|2||NCT02880735||Recruiting||Ventilatory Response After Non Invasive Ventilation in Type 1 Myotonic Dystrophy||
||27||All||18 Years and older (Adult, Older Adult)||NCT02880735||C46-15||September 2016||December 2018||April 2019||August 26, 2016||July 11, 2018||
† Study has passed its completion date and status has not been verified in more than two years.