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Recruiting, Not yet recruiting, Available Studies | "Rett Syndrome"
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Recruiting, Not yet recruiting, Available Studies | "Rett Syndrome" (10 records)
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1 | NCT03059160 | Not yet recruiting | Open Label Trial of Triheptanoin (UX007) in Treatment of Rett Syndrome. |
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Interventional | Phase 2 |
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Other / Industry |
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10 | Female | 5 Years to 18 Years (Child, Adult) | NCT03059160 | 3027-16-SMC | UX007 | April 1, 2017 | April 1, 2018 | August 1, 2018 | February 23, 2017 | February 23, 2017 | ||
2 | NCT03196323 | Recruiting | Development of a Behavioral Outcome Measure for Rett Syndrome (RettBe) |
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Observational |
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Other / NIH |
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400 | Female | 3 Years to 18 Years (Child, Adult) | NCT03196323 | RTT5214 | June 1, 2017 | March 2019 | March 2019 | June 22, 2017 | June 26, 2017 |
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3 | NCT02903056 | Recruiting | The Findings of MR Imaging in Rett Syndrome |
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Observational |
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Other |
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100 | All | 3 Years to 30 Years (Child, Adult) | NCT02903056 | 201510011RINC | March 2016 | September 2017 | September 2017 | September 16, 2016 | September 16, 2016 |
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4 | NCT02696044 | Recruiting | Treatment of Mitochondrial Dysfunction in Rett Syndrome With Triheptanoin |
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Interventional | Phase 2 |
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Other / Industry |
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12 | Female | 2 Years and older (Child, Adult, Senior) | NCT02696044 | IRB00085194 | June 2016 | February 2019 | February 2019 | March 2, 2016 | February 7, 2018 |
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5 | NCT02790034 | Recruiting | Evaluation of the Efficacy, Safety, and Tolerability of Sarizotan in Rett Syndrome With Respiratory Symptoms |
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Interventional | Phase 2 Phase 3 |
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Industry |
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129 | All | 4 Years and older (Child, Adult, Senior) | NCT02790034 | Sarizotan/001/II/2015 | August 2016 | July 2018 | December 2018 | June 3, 2016 | April 19, 2018 |
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6 | NCT02738281 | Recruiting | Natural History of Rett Syndrome & Related Disorders |
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Observational |
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Other / NIH |
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1200 | All | Child, Adult, Senior | NCT02738281 | RDCRN 5211 | November 2015 | July 2019 | December 2019 | April 14, 2016 | April 5, 2018 |
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7 | NCT02705677 | Recruiting | Biobanking of Rett Syndrome and Related Disorders |
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Observational |
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Other / NIH |
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1200 | All | Child, Adult, Senior | NCT02705677 | RDCRN # 5213 U54HD061222 |
September 1, 2017 | July 2019 | December 2019 | March 10, 2016 | April 20, 2018 |
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8 | NCT03077308 | Recruiting | Rare Diseases Clinical Research Network: Neurophysiological Correlates |
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Observational |
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Other / NIH |
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250 | All | 2 Years to 65 Years (Child, Adult) | NCT03077308 | RDCRN 5212 | January 2, 2017 | July 31, 2019 | July 31, 2019 | March 10, 2017 | April 20, 2018 |
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9 | NCT03259971 | Recruiting | The Role of Probiotics PS128 in Movement Disorders |
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Interventional | Not Applicable |
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Other |
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500 | All | 1 Year to 50 Years (Child, Adult) | NCT03259971 | 201703061MIPA | August 25, 2017 | August 20, 2019 | August 20, 2020 | August 24, 2017 | November 27, 2017 |
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10 | NCT03276195 | Recruiting | Studies in Patients With Tuberous Sclerosis Complex |
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Observational |
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Other / U.S. Fed |
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1000 | All | Child, Adult, Senior | NCT03276195 | vnarayanan15-016 | May 2016 | December 2019 | December 2021 | September 8, 2017 | March 13, 2018 |
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† Study has passed its completion date and status has not been verified in more than two years.