Comment Period Extended to 3/23/2015 for Notice of Proposed Rulemaking (NPRM) for FDAAA 801 and NIH Draft Reporting Policy for NIH-Funded Trials
105 studies found for:    Open Studies | "Muscular Dystrophies"
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Rank Status Study
21 Recruiting A Phase I/II Study of PRO053 in Subjects With Duchenne Muscular Dystrophy (DMD)
Condition: Duchenne Muscular Dystrophy
Interventions: Drug: Cohort 1;   Drug: Cohort 2;   Drug: 48-week treatment phase
22 Recruiting L-citrulline and Metformin in Duchenne's Muscular Dystrophy
Condition: Duchenne's Muscular Dystrophy (DMD)
Interventions: Drug: 750 mg metformin and 7.5 g L-citrulline daily p.o.;   Drug: Placebo
23 Recruiting A Phase 2 Study to Evaluate the Safety, Efficacy, Pharmacokinetics and Pharmacodynamics of PF-06252616 in Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Biological: PF-06252616
24 Recruiting Stem Cell Therapy in Muscular Dystrophy
Condition: Muscular Dystrophy
Intervention: Biological: Stem Cell
25 Recruiting Establishment of Phenotypic Profiles of Muscular Dystrophies for Understanding Disease Progression, Diagnosis and Development of New Therapies
Conditions: Muscular Dystrophies;   Muscular Dystrophy
Intervention:
26 Recruiting A Study to Test Lung Stretch Therapy (Hyperinsufflation) to Slow the Rate of Decline in Children With Collagen VI Muscular Dystrophy
Conditions: Congenital Muscular Dystrophy;   Collagen VI Deficiency
Intervention: Other: Hyperinsufflation therapy
27 Recruiting DuchenneConnect Registry
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Intervention:
28 Recruiting Ramipril Versus Carvedilol in Duchenne and Becker Patients
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Interventions: Drug: carvedilol;   Drug: ramipril
29 Recruiting Congenital Muscle Disease Study of Patient and Family Reported Medical Information
Conditions: Muscular Dystrophy;   Congenital Muscular Dystrophy;   Fukutin-related Protein Gene;   Limb Girdle;   FKRP Gene;   Childhood Onset LGMD;   Adult Onset LGMD;   POMT1;   POMT2;   POMGnT1;   LARGE;   Alpha Dystroglycan;   Dystroglycanopathy;   Centronuclear;   Multiminicore;   Multicore;   Minicore;   Congenital Fiber Type Disproportion;   Myotubular;   Nemaline;   Congenital Myopathy;   Neuromuscular;   Rigid Spine;   Phenotype-Genotype Correlation;   Cough Assisted Device;   Neuromuscular Disease;   Respiratory Exacerbation;   Invasive Ventilation;   Chest Physiotherapy;   Congenital Myopathies;   Genetic Mutations;   Hypertrophic Cardiomyopathy;   Wheelchair Use;   Cataract;   Opthalmoplegia;   Ullrich Congenital Muscular Dystrophy;   Intermediate Collagen VI Myopathy;   Laminin Alpha 2 Related Congenital Muscular Dystrophy;   MDC1A;   Merosin Deficient Congenital Muscular Dystrophy;   Congenital Muscular Dystrophy Undiagnosed;   Congenital Muscular Dystrophy Merosin Positive;   Walker Warburg Syndrome;   Muscle Eye Brain Disease;   Fukuyama;   Integrin Alpha 7 Deficiency;   Integrin Alpha 9 Deficiency;   Laminopathy;   Lamin AC;   SEPN 1 Related Myopathies;   Bethlem Myopathy;   Dystroglycanopathies;   LGMD2K;   LGMD2I;   LGMD2L;   LGMD2N;   Actin Aggregation Myopathy;   Cap Disease;   Central Core Disease;   Centronuclear Myopathy;   Core Rod Myopathy;   Hyaline Body Myopathy;   Multiminicore Myopathy;   Myotubular Myopathy;   Nemaline Myopathy;   Tubular Aggregate Myopathy;   Zebra Body Disease Myopathy;   Congenital Myopathy Other;   Reducing Body Myopathy;   Sarcotubular Myopathy;   Spheroid Body Myopathy
Intervention:
30 Recruiting Assessment of Cardiopulmonary Function in Duchenne Muscular Dystrophy
Condition: Muscular Dystrophy, Duchenne
Interventions: Other: Magnetic Resonance Imaging (MRI);   Other: Pulmonary Function Testing (PFT);   Other: Metabolic Exercise Testing using stationary bicycle;   Other: Echocardiogram
31 Recruiting Duchenne Muscular Dystrophy < 18y in Norway: Genotype/Phenotype, Growth, Puberty, Bone Health and Quality of Life.
Condition: Duchenne Muscular Dystrophy
Intervention:
32 Recruiting Becker Muscular Dystrophy - A Natural History Study to Predict Efficacy of Exon Skipping
Condition: Becker Muscular Dystrophy
Intervention:
33 Recruiting Transplantation of Myoblasts to Duchenne Muscular Dystrophy (DMD) Patients
Condition: Duchenne Muscular Dystrophy
Intervention: Biological: Myoblast transplantation
34 Recruiting A Study of TAS-205 for Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Interventions: Drug: TAS-205;   Drug: Placebo
35 Recruiting Safety Study of Eteplirsen to Treat Advanced Stage Duchenne Muscular Dystrophy
Condition: Muscular Dystrophy, Duchenne
Intervention: Drug: eteplirsen
36 Recruiting Therapeutic Potential for Aldosterone Inhibition in Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Interventions: Drug: Eplerenone;   Drug: Spironolactone
37 Recruiting Efficacy of Umbilical Cord Mesenchymal Stem Cells in Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Biological: Umbilical Cord Mesenchymal Stem Cell
38 Recruiting Whole Body Vibration Therapy in Boys With Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Device: Whole Body Vibration Therapy
39 Recruiting Effect of Aerobic Training in Patients With Oculopharyngeal Muscular Dystrophy
Condition: Oculopharyngeal Muscular Dystrophy
Intervention: Behavioral: Exercise
40 Unknown  This is a Study to Get More Information About Non Ambulatory Boys & Men With Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention:

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