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Recruiting, Not yet recruiting, Available Studies | "Muscular Atrophy, Spinal"
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Recruiting, Not yet recruiting, Available Studies | "Muscular Atrophy, Spinal" (30 records)
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1 | NCT02913482 | Recruiting | Investigate Safety, Tolerability, PK, PD and Efficacy of RO7034067 in Infants With Type1 Spinal Muscular Atrophy |
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Interventional | Phase 2 Phase 3 |
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Industry |
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48 | All | 1 Month to 7 Months (Child) | NCT02913482 | BP39056 2016-000778-40 |
FIREFISH | December 24, 2016 | September 2, 2020 | September 2, 2020 | September 23, 2016 | April 9, 2018 |
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2 | NCT02908685 | Recruiting | A Study to Investigate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Efficacy of RO7034067 in Type 2 and 3 Spinal Muscular Atrophy (SMA) Participants |
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Interventional | Phase 2 Phase 3 |
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Industry |
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219 | All | 2 Years to 25 Years (Child, Adult) | NCT02908685 | BP39055 2016-000750-35 |
SUNFISH | October 20, 2016 | May 31, 2019 | July 16, 2020 | September 21, 2016 | April 13, 2018 |
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3 | NCT03217578 | Recruiting | Neonatal Spinal Muscular Atrophy (SMA) Screening |
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Observational |
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Other |
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250000 | All | up to 2 Weeks (Child) | NCT03217578 | SMA-NBS001 | SMA | September 1, 2017 | December 31, 2019 | December 31, 2019 | July 14, 2017 | November 13, 2017 |
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4 | NCT02268552 | Recruiting | An Open Label Study of LMI070 (Branaplam) in Type 1 Spinal Muscular Atrophy (SMA) |
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Interventional | Phase 1 Phase 2 |
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Industry |
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44 | All | up to 182 Days (Child) | NCT02268552 | CLMI070X2201 | April 2, 2015 | November 14, 2019 | November 14, 2019 | October 20, 2014 | March 29, 2018 |
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5 | NCT03339830 | Recruiting | European Registry of Patients With Infantile-onset Spinal Muscular Atrophy |
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Observational |
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Other |
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100 | All | Child, Adult, Senior | NCT03339830 | IO-SMA-Registry 2017-A02291-52 |
October 10, 2017 | December 1, 2022 | December 1, 2022 | November 13, 2017 | January 24, 2018 |
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6 | NCT03395795 | Not yet recruiting | Trial Evaluating the Interest of Noninvasive Ventilation in NAVA Mode in Respiratory Decompensations Children With Infantile Spinal Muscular Atrophy Type II |
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Interventional | Not Applicable |
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Other |
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20 | All | 1 Year to 18 Years (Child, Adult) | NCT03395795 | P160941J IDRCB 2017-A02785-48 |
NAVASI | January 2018 | January 2020 | January 2020 | January 10, 2018 | January 10, 2018 |
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7 | NCT03056144 | Recruiting | Whole Body Vibration Therapy in Children With Spinal Muscular Atrophy |
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Interventional | Not Applicable |
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Other |
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10 | All | 6 Years to 18 Years (Child, Adult) | NCT03056144 | YBPA | August 1, 2017 | March 31, 2019 | March 31, 2019 | February 17, 2017 | August 10, 2017 |
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8 | NCT03381729 | Recruiting | Study of Intrathecal Administration of AVXS-101 for Spinal Muscular Atrophy |
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Interventional | Phase 1 |
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Industry |
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27 | All | up to 60 Months (Child) | NCT03381729 | AVXS-101-CL-102 | STRONG | December 14, 2017 | August 30, 2019 | August 30, 2019 | December 22, 2017 | February 12, 2018 |
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9 | NCT02831296 | Recruiting | Prospective Evaluation of Infants With Spinal Muscular Atrophy: |
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Observational |
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Other / NIH |
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200 | All | Child, Adult, Senior | NCT02831296 | 2015P001934 R01HD069045 |
SPOTSMA | February 2016 | March 2022 | July 13, 2016 | April 19, 2017 |
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10 | NCT03505099 | Recruiting New |
Pre-Symptomatic Study of Intravenous AVXS-101 in Spinal Muscular Atrophy (SMA) for Patients With Multiple Copies of SMN2 |
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Interventional | Phase 3 |
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Industry |
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44 | All | up to 42 Days (Child) | NCT03505099 | AVXS-101-CL-304 | SPR1NT | April 10, 2018 | October 2020 | April 2023 | April 23, 2018 | April 23, 2018 |
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11 | NCT03032172 | Recruiting | A Study of RO7034067 in Adult and Pediatric Participants With Spinal Muscular Atrophy |
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Interventional | Phase 2 |
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Industry |
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24 | All | 12 Years to 60 Years (Child, Adult) | NCT03032172 | BP39054 2016-004184-39 |
Jewelfish | March 3, 2017 | April 5, 2019 | December 1, 2020 | January 26, 2017 | April 24, 2018 |
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12 | NCT02865109 | Available | Expanded Access Program (EAP) for Nusinersen in Participants With Infantile-onset (Consistent With Type 1) Spinal Muscular Atrophy (SMA) |
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Expanded Access |
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Industry | All | Child, Adult, Senior | NCT02865109 | 232-SM-901 | August 12, 2016 | April 9, 2018 |
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13 | NCT02876094 | Not yet recruiting | Effect of Low-Dose Celecoxib on SMN2 in Patients With Spinal Muscular Atrophy |
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Interventional | Phase 2 |
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Other |
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12 | All | 2 Years to 80 Years (Child, Adult, Senior) | NCT02876094 | 15/22E | SMA | August 2017 | July 2018 | July 2018 | August 23, 2016 | August 2, 2017 |
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14 | NCT03223051 | Recruiting | Development of a Space Exploration Assessment for Children With Spinal Muscular Atrophy |
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Interventional | Not Applicable |
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Other |
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30 | All | 3 Years to 16 Years (Child) | NCT03223051 | 2017-A01017-46 | ExplorASI | September 7, 2017 | September 7, 2017 | September 2020 | July 19, 2017 | January 25, 2018 |
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15 | NCT02061189 | Recruiting | Pilot Study of an Innovative Physiotherapy in Patients With Infantile Spinal Muscular Atrophy (SMA) |
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Interventional | Not Applicable |
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Other |
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30 | All | 5 Years to 10 Years (Child) | NCT02061189 | P120124 2013-A01331-44 |
ExerASI | March 2014 | December 2017 | October 2018 | February 12, 2014 | November 20, 2017 |
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16 | NCT03300869 | Recruiting | Natural History of Types 2 and 3 SMA in Taiwan |
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Observational |
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Other / Industry |
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300 | All | 6 Months to 70 Years (Child, Adult, Senior) | NCT03300869 | SMA_RV | September 1, 2017 | December 2019 | December 2019 | October 4, 2017 | November 13, 2017 |
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17 | NCT03306277 | Recruiting | Gene Replacement Therapy Clinical Trial for Patients With Spinal Muscular Atrophy Type 1 |
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Interventional | Phase 3 |
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Industry |
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15 | All | up to 180 Days (Child) | NCT03306277 | AVXS-101-CL-303 | STR1VE | September 29, 2017 | March 31, 2020 | March 31, 2020 | October 11, 2017 | February 28, 2018 |
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18 | NCT02550691 | Recruiting | Identification of a Biomarker Associated With Cis-duplication of the SMN1 Gene |
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Interventional | Not Applicable |
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Other |
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311 | All | 18 Years and older (Adult, Senior) | NCT02550691 | 2015/092/HP | BADGES | December 2015 | December 2017 | December 2017 | September 15, 2015 | August 30, 2017 |
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19 | NCT02895789 | Recruiting | Oxidative Capacity and Exercise Tolerance in Ambulatory SMA |
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Observational |
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Other / NIH |
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42 | All | 8 Years to 55 Years (Child, Adult) | NCT02895789 | AAAQ9447 1K01HD084690-01A1 |
November 2016 | July 2019 | May 2020 | September 12, 2016 | November 6, 2017 |
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20 | NCT03461289 | Not yet recruiting | Single-Dose Gene Replacement Therapy Clinical Trial for Patients With Spinal Muscular Atrophy Type 1 |
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Interventional | Phase 3 |
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Industry |
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30 | All | up to 6 Months (Child) | NCT03461289 | AVXS-101-CL-302 | STRIVE-EU | May 2018 | November 2020 | November 2020 | March 12, 2018 | April 25, 2018 |
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21 | NCT02855112 | Recruiting | Allogeneic Adipose Derived Stem Cells for Werdnig Hoffman Patients |
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Interventional | Phase 1 Phase 2 |
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Other |
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10 | All | 5 Months to 12 Months (Child) | NCT02855112 | 94-01-87-28524 | June 2015 | December 2016 | July 2017 | August 4, 2016 | August 4, 2016 |
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22 | NCT02532244 | Recruiting | Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases |
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Observational |
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Other |
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300 | All | 6 Months and older (Child, Adult, Senior) | NCT02532244 | 764456 | June 2015 | December 2022 | December 2022 | August 25, 2015 | August 25, 2015 |
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23 | NCT03489278 | Recruiting New |
Clinical Procedures to Support Research |
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Observational |
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Other / NIH |
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1200 | All | 18 Years and older (Adult, Senior) | NCT03489278 | 20170785 U54NS092091 |
CAPTURE | February 15, 2018 | January 2021 | January 2021 | April 5, 2018 | April 5, 2018 |
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24 | NCT02124616 | Recruiting | National Registry for Egyptian Pediatric Neuromuscular Diseases |
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Observational |
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Other |
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200 | All | 1 Month to 18 Years (Child, Adult) | NCT02124616 | EGYPT PED-NMD 2014 | April 2014 | April 2020 | December 2020 | April 28, 2014 | April 28, 2014 |
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25 | NCT02327845 | Recruiting | Phenotype, Genotype & Biomarkers in ALS and Related Disorders |
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Observational |
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Other / NIH |
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700 | All | Child, Adult, Senior | NCT02327845 | U54NS092091 | April 2015 | August 2019 | August 2019 | December 30, 2014 | January 23, 2018 |
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26 | NCT02574390 | Recruiting | Answer ALS: Individualized Initiative for ALS Discovery |
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Observational |
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Other |
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1000 | All | 18 Years to 100 Years (Adult, Senior) | NCT02574390 | IRB00082277 | AnswerALS | December 2015 | January 2019 | July 2019 | October 12, 2015 | April 9, 2018 |
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27 | NCT02124057 | Recruiting | Study of Hepatic Function in Patients With Spinal and Bulbar Muscular Atrophy |
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Observational |
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NIH |
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75 | All | 18 Years and older (Adult, Senior) | NCT02124057 | 140099 14-N-0099 |
April 25, 2014 | January 1, 2019 | January 1, 2019 | April 28, 2014 | March 29, 2018 |
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28 | NCT02795897 | Recruiting | Genomic Translation for ALS Care |
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Observational |
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Other / Industry |
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1500 | All | 18 Years to 80 Years (Adult, Senior) | NCT02795897 | AAAQ7026 | GTAC | November 2016 | June 2019 | November 2020 | June 10, 2016 | July 21, 2017 |
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29 | NCT03196375 | Recruiting | A Study to Assess FLX-787 in Subjects With Motor Neuron Disease Experiencing Muscle Cramps. |
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Interventional | Phase 2 |
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Industry |
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120 | All | 18 Years and older (Adult, Senior) | NCT03196375 | FLX-787-203 | July 28, 2017 | June 2018 | June 2018 | June 22, 2017 | March 22, 2018 |
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30 | NCT00874783 | Recruiting | Development of iPS From Donated Somatic Cells of Patients With Neurological Diseases |
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Observational |
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Other |
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120 | All | 18 Years and older (Adult, Senior) | NCT00874783 | 0599-08-HMO-CTIL | April 2009 | December 2025 | December 2025 | April 3, 2009 | November 28, 2017 |
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† Study has passed its completion date and status has not been verified in more than two years.