29 studies found for:    Open Studies | "Muscular Atrophy, Spinal"
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Open Studies | "Muscular Atrophy, Spinal" (29 records)
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Rank Status Study
1 Recruiting An Open Label Study of LMI070 in Type 1 Spinal Muscular Atrophy (SMA)
Condition: Muscular Atrophy, Spinal [C10.668.475]
Intervention: Drug: LMI070
2 Recruiting Prospective Study of the Natural History of Patients With Type 2 and 3 Spinal Muscular Atrophy
Conditions: Type 2 Spinal Muscular Atrophy;   Type 3 Spinal Muscular Atrophy
Interventions: Other: Strength, function and activity measurements;   Other: Muscle MRI;   Other: Electrophysiology measurements;   Other: Blood sampling for biomarker analysis
3 Recruiting Palliative Care in Spinal Muscular Atrophy (SMA) 1
Condition: Spinal Muscular Atrophy 1
Intervention: Other: Follow-up diary and questionnaire
4 Recruiting International SMA Patient Registry
Condition: Muscular Atrophy, Spinal
Intervention:
5 Recruiting Pilot Study of an Innovative Physiotherapy in Patients With Infantile Spinal Muscular Atrophy (SMA)
Condition: Infantile Spinal Muscular Atrophy of Type 2 or 3
Intervention: Other: Physical exercise in a swimming pool during 6 months
6 Unknown  Infants With Spinal Muscular Atrophy Type I
Condition: Spinal Muscular Atrophy
Intervention:
7 Recruiting A Study to Assess the Efficacy and Safety of ISIS-SMN Rx in Infants With Spinal Muscular Atrophy
Condition: Spinal Muscular Atrophy
Interventions: Drug: ISIS-SMN Rx;   Procedure: Sham procedure
8 Recruiting Safety and Efficacy Study of Pyridostigmine on Patients With Spinal Muscular Atrophy Type 3
Condition: Spinal Muscular Atrophy Type 3
Intervention: Drug: Pyridostigmine Bromide
9 Recruiting A Study to Assess the Efficacy and Safety of ISIS-SMN Rx in Patients With Later-onset Spinal Muscular Atrophy
Condition: Spinal Muscular Atrophy
Interventions: Drug: ISIS-SMN Rx;   Procedure: Sham procedure
10 Recruiting A Study to Assess the Safety and Tolerability of ISIS 396443 (ISIS SMNRx) in Participants With Spinal Muscular Atrophy (SMA).
Condition: Spinal Muscular Atrophy
Interventions: Drug: ISIS-SMN RA;   Procedure: Sham Procedure
11 Recruiting Gene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1
Condition: Spinal Muscular Atrophy 1
Intervention: Biological: scAAV9.CB.SMN
12 Recruiting Valproate and Levocarnitine in Children With Spinal Muscular Atrophy
Condition: Spinal Muscular Atrophy
Interventions: Drug: Valproate, Levocarnitine;   Drug: Placebo
13 Recruiting A Study of Multiple Doses of ISIS SMNRx (ISIS 396443) Delivered to Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy
Condition: Spinal Muscular Atrophy
Intervention: Drug: ISIS SMNRx (ISIS 396443)
14 Unknown  Motor Development and Orthoses in Spinal Muscular Atrophy (SMA)
Condition: Spinal Muscular Atrophy
Intervention:
15 Not yet recruiting Study of Feasibility to Reliably Measure Functional Abilities' Changes in Nonambulant Neuromuscular Patients Without Trial Site Visiting
Conditions: Spinal Muscular Atrophy;   Neuromuscular Disorders
Intervention: Other: Direct current stimulation of cervical spinal cord
16 Recruiting Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases
Conditions: Spinal Muscular Atrophy;   Charcot-Marie-Tooth Disease;   Muscular Dystrophy;   Spinal Muscular Atrophy With Respiratory Distress 1;   Amyotrophic Lateral Sclerosis;   Motor Neuron Disease;   Neuromuscular Disease;   Peroneal Muscular Atrophy;   Fragile X Syndrome
Intervention: Other: sample collection
17 Not yet recruiting Effects of Standing on Non-Ambulatory Children With Neuromuscular Conditions
Conditions: Osteopenia;   Spinal Muscular Atrophy;   Cerebral Palsy;   Muscular Dystrophy;   Spina Bifida;   Rett Syndrome
Intervention: Other: Assisted Standing Treatment Program
18 Recruiting National Registry for Egyptian Pediatric Neuromuscular Diseases
Conditions: Spinal Muscular Atrophy;   Muscular Dystrophy;   Muscle Diseases;   Myasthenic Syndromes;   Polyneuropathies
Intervention:
19 Unknown  Quantitative Analysis of SMN1 and SMN2 Gene Based on DHPLC System
Condition: Spinal Muscular Atrophy
Intervention:
20 Unknown  Establishing Novel Detection Techniques for Various Genetic-Related Diseases by Applying DHPLC Platform.
Conditions: Spinal Muscular Atrophy;   Neonatal Hyperbilirubinemia;   Colon Cancer
Intervention:

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Indicates status has not been verified in more than two years