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38 studies found for:    Open Studies | "Mucopolysaccharidoses"
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Study Details
Participant Details
Identifiers
Dates
Rank Status Study
1 Recruiting A Study of JR-141 in Patients With Mucopolysaccharidosis Type II
Condition: Mucopolysaccharidosis II
Intervention: Drug: JR-141
2 Recruiting Mucopolysaccharidosis I (MPS I) Registry
Condition: Mucopolysaccharidosis I (MPS I)
Intervention:
3 Not yet recruiting Mucopolysaccharidosis (MPS) Screening in a High-Risk Population With Previous Surgical Repair or Presence of Inguinal and/or Umbilical Hernia Combined With Pediatric ENT Surgery or Bronchoscopy
Condition: Mucopolysaccharidoses
Intervention:
4 Recruiting Effects of Adalimumab in Mucopolysaccharidosis Types I, II and VI
Conditions: Mucopolysaccharidosis Type I;   Mucopolysaccharidosis Type II;   Mucopolysaccharidosis Type VI
Interventions: Drug: Adalimumab;   Other: Placebo
5 Recruiting A Treatment Study of Mucopolysaccharidosis Type IIIB
Conditions: MPS III B;   Mucopolysaccharidosis Type IIIB
Intervention: Drug: BMN 250
6 Recruiting Natural History Study of Patients With MPS IIIA
Condition: Mucopolysaccharidosis IIIA
Intervention:
7 Recruiting Ascending Dose Study of Genome Editing by the Zinc Finger Nuclease (ZFN) Therapeutic SB-913 in Subjects With MPS II
Condition: Mucopolysaccharidosis II
Intervention: Biological: SB-913
8 Not yet recruiting Study of Idursulfase-beta (GC1111) in Hunter Syndrome
Condition: Mucopolysaccharidosis II
Interventions: Biological: idursulfase beta;   Biological: idursulfase
9 Recruiting Safety and Dose Ranging Study of Insulin Receptor MoAb-IDS Fusion Protein in Patients With Hunter Syndrome
Condition: Mucopolysaccharidosis II
Intervention: Drug: AGT-182
10 Recruiting Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Condition: Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome)
Intervention:
11 Recruiting Phase I/II Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH for Mucopolysaccharidosis (MPS) IIIA
Condition: Mucopolysaccharidosis Type 3 A Sanfilippo Syndrome
Intervention: Biological: scAAV9.U1a.hSGSH
12 Recruiting A Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)
Conditions: Mucopolysaccharidosis Type IIIB;   Mucopolysaccharidosis Type 3 B;   MPS III B;   MPS 3 B
Intervention:
13 Not yet recruiting Study to Evaluate the Safety and Efficacy of Adalimumab in MPS I and II
Conditions: Mucopolysaccharidosis I;   Mucopolysaccharidosis II
Interventions: Drug: Adalimumab Injection [Humira];   Drug: Saline Solution for Injection
14 Recruiting A Study of the Effect of Aldurazyme® (Laronidase) Treatment on Lactation in Female Patients With Mucopolysaccharidosis I (MPS I) and Their Breastfed Infants
Conditions: Mucopolysaccharidosis I;   Hurler's Syndrome;   Hurler-Scheie Syndrome;   Scheie
Intervention: Biological: Aldurazyme (laronidase)
15 Not yet recruiting Parental Coping With Challenging Behavior in Mucopolysaccharidosis Type I-III
Conditions: Mucopolysaccharidosis Type I;   Mucopolysaccharidosis Type II;   Mucopolysaccharidosis Type III;   Behavior Disorders;   Coping Behavior
Intervention: Other: This is an observational study
16 Recruiting New Imaging Technology to Assess Effect of Enzyme Replacment Therapy on Eye Disease Progession in Mucopolysacchardiosis
Condition: Mucopolysaccharidoses
Intervention:
17 Recruiting The Long-term Safety Study of Idursulfase-beta in Hunter Syndrome(Mucopolysaccharidosis II) Patients
Condition: Hunter Syndrome
Intervention:
18 Recruiting Pregnancy With Morquio Syndrome - What Are Patients' Perspectives and Has ERT Changed Them?
Conditions: Morquio Disease;   MPS - Mucopolysaccharidosis
Intervention: Other: Interview
19 Recruiting Biomarker for Hunter Disease
Conditions: Lysosomal Storage Diseases;   Hunter Disease;   Mucopolysaccharidoses
Intervention:
20 Recruiting Laronidase (Aldurazyme TM) Enzyme Replacement Therapy With Hematopoietic Stem Cell Transplant for Hurler Syndrome
Conditions: Mucopolysaccharidosis Type IH;   MPS I;   Hurler Syndrome
Intervention: Drug: Laronidase

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Study has passed its completion date and status has not been verified in more than two years.