7 studies found for: Open Studies | "Leukodystrophy, Metachromatic"
Intracerebral Gene Therapy for Children With Early Onset Forms of Metachromatic Leukodystrophy
Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy
Biomarker for Metachromatic Leukodystrophy Disease
UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
Human Placental-Derived Stem Cell Transplantation
MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
Reduced Intensity Conditioning in Patients Aged ≤35 With Non-Malignant Disorders Undergoing UCBT, BMT, or PBSCT
† Study has passed its completion date and status has not been verified in more than two years.