9 studies found for: Open Studies | "Leukodystrophy, Globoid Cell"
Krabbe Disease Global Patient Registry
Biomarker for Krabbe Disease
|3||Not yet recruiting||
Safety and Exploratory Efficacy of HSC835 in Patients With Inherited Metabolic Disorders (IMD)
Lysosomal Storage Disease: Health, Development, and Functional Outcome Surveillance in Preschool Children
UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
Genetic Characterization of Movement Disorders and Dementias
Human Placental-Derived Stem Cell Transplantation
Reduced Intensity Conditioning in Patients Aged ≤35 With Non-Malignant Disorders Undergoing UCBT, BMT, or PBSCT
† Study has passed its completion date and status has not been verified in more than two years.