26 studies found for: Open Studies | "Gaucher Disease"
A Study of the Effects of Hepatic Impairment on the Pharmacokinetics and Tolerability of Eliglustat Tartrate
Clinical and Basic Investigations Into Erdheim Chester Disease
Nervous System Degeneration in Glycosphingolipid Storage Disorders
Human Placental-Derived Stem Cell Transplantation
Molecular and Cellular Mechanisms of Lysosomal Storage Diseases
Reduced Intensity Conditioning in Patients Aged ≤35 With Non-Malignant Disorders Undergoing UCBT, BMT, or PBSCT
† Indicates status has not been verified in more than two years