12 studies found for: Open Studies | "Adrenoleukodystrophy"
Newborn Screening for Adrenoleukodystrophy
Expanded Access for Lorenzo's Oil (GTO/GTE) in Adrenoleukodystrophy
A Phase 2/3 Study of the Efficacy and Safety of Hematopoietic Stem Cells Transduced With Lenti-D Lentiviral Vector for the Treatment of Cerebral Adrenoleukodystrophy (CALD)
A Pilot Study of Vitamin D in Boys With X-linked Adrenoleukodystrophy
Observational Study to Evaluate Allogeneic HSCT Outcomes for Cerebral Adrenoleukodystrophy (CALD)
|6||Not yet recruiting||
Early Diagnosis Of Childhood Cerebral ALD
Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy
UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
Human Placental-Derived Stem Cell Transplantation
Expanded Access to T-cell Depleted Haplo-Identical Stem Cells for Patients Receiving Haplo-Identical and Unrelated Cord Blood Transplants
Reduced Intensity Conditioning in Patients Aged ≤35 With Non-Malignant Disorders Undergoing UCBT, BMT, or PBSCT
† Study has passed its completion date and status has not been verified in more than two years.