The Natural History and Pathogenesis of Mucolipidosis Type IV
The Natural History of Mucolipidosis Type IV
An Open Label, Single Dose, Three Part Study to Assess the Effects of Rolapitant (2 mg/mL IV Solution) on the Pharmacokinetics of Digoxin; Sulfasalazine; and the Cooperstown Cocktail (Midazolam, Omeprazole, Warfarin, Caffeine, and Dextromethorphan in Healthy Subjects
Biomarker for Mucolipidosis Disorder Type I, II, III or IV
Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
Biomarker for Glycogen Storage Diseases
† Study has passed its completion date and status has not been verified in more than two years.