Glycogen Storage Disease Type IV Database
Triheptanoin Treatment Trial for Patients With Adult Polyglucosan Body Disease
Biomarker for Glycogen Storage Diseases
Fat and Sugar Metabolism During Exercise in Patients With Metabolic Myopathy
|5||Not yet recruiting||
VAL-1221 Delivered Intravenously in Ambulatory and Ventilator-free Patients With Late-Onset Pompe Disease
† Study has passed its completion date and status has not been verified in more than two years.