3 studies found for: "nemaline myopathy" OR "Myopathies, Nemaline"
Congenital Muscle Disease Study of Patient and Family Reported Medical Information
|2||Enrolling by invitation||
Treatment of TNNT1-Myopathy With L-Tyrosine.
Molecular and Genetic Studies of Congenital Myopathies
† Indicates status has not been verified in more than two years