Comment Period Extended to 3/23/2015 for Notice of Proposed Rulemaking (NPRM) for FDAAA 801 and NIH Draft Reporting Policy for NIH-Funded Trials
94 studies found for:    "mucopolysaccharidosis type IV"
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Rank Status Study
21 Active, not recruiting An Efficacy and Safety Trial of Intravenous Zoledronic Acid in Infants Less Than One Year of Age, With Severe Osteogenesis Imperfecta
Condition: Osteogenesis Imperfecta
Intervention: Drug: Zoledronic Acid
22 Recruiting Evaluation of Skeletal Maturity for Slipped Capital Femoral Epiphysis
Condition: Slipped Capital Femoral Epiphysis
Intervention: Radiation: Radiographic skeletal age assessment
23 Active, not recruiting Pamidronate to Treat Osteogenesis Imperfecta in Children
Condition: Osteogenesis Imperfecta
Intervention: Drug: Pamidronate (Aredia)
24 Recruiting MT2013-31:Allo BMT for Metabolic Disorders, Osteopetrosis and Males With Rett Syndrome
Conditions: Mucopolysaccharidosis I;   Mucopolysaccharidosis II;   Mucopolysaccharidosis VI;   Mucopolysaccharidosis VII;   Hurler Syndrome;   Hunter Syndrome;   Maroteaux Lamy Syndrome;   Sly Syndrome;   Glycoprotein Metabolic Disorders;   Alpha Mannosidosis;   Fucosidosis;   Aspartylglucosaminuria;   Adrenoleukodystrophy;   Peroxisomal Disorders;   Osteopetrosis;   Rett Syndrome;   Sphingolipidosis;   Gangliosidosis;   Globoid Cell Leukodystrophy;   Metachromatic Leukodystrophy;   Niemann Pick B;   Niemann Pick C Subtype 2;   I-cell Disease
Interventions: Procedure: blood stem cell transplant;   Drug: Rabbit Anti-Thymocyte Globulin (ATG);   Drug: Fludarabine;   Drug: Busulfan;   Drug: Cyclophosphamide;   Drug: Cyclosporine A (CSA);   Drug: Methylprednisolone;   Drug: Mycophenolate Mofetil (MMF);   Drug: Granulocyte-Colony Stimulating Factor (G-CSF);   Drug: Granulocyte-Macrophage Colony-Stimulating Factor (GM-CSF);   Drug: N-acetylcysteine;   Drug: Celecoxib;   Drug: Vitamin E;   Drug: Alpha Lipoic Acid
25 Active, not recruiting C-Type Natriuretic Peptide and Achondroplasia
Conditions: Achondroplasia;   Hypochondroplasia
Intervention:
26 Unknown  Histamine Responsiveness in McCune-Albright Syndrome
Condition: McCune-Albright Syndrome
Intervention:
27 Active, not recruiting A Study to Assess the Long-term Performance of SmartSet® HV and SmartSet® GHV Bone Cements in Primary Total Hip Replacement
Conditions: Rheumatoid Arthritis;   Osteoarthritis;   Post-traumatic Arthritis;   Collagen Disorders;   Avascular Necrosis;   Traumatic Femoral Fractures;   Nonunion of Femoral Fractures;   Congenital Hip Dysplasia;   Slipped Capital Femoral Epiphysis
Interventions: Device: SmartSet® HV bone cement;   Device: SmartSet® GHV bone cement
28 Completed Translational Therapy in Patients With Osteogenesis Imperfecta - A Pilot Trial on Treatment With the Rankl-Antibody Denosumab
Condition: Osteogenesis Imperfecta
Intervention: Drug: Denosumab
29 Unknown  Hematopoietic Stem Cell Transplantation for Malignant Infantile Osteopetrosis
Condition: Osteopetrosis
Interventions: Drug: Busulfan, Cyclophosphamide, Thymoglobulin, Fludarabine (Conditioning regimen);   Procedure: Stem Cell Transplantation;   Drug: Cyclosporin, Methotrexate (GVHD prophylaxis)
30 Unknown  Antioxidant Supplementation in Patients With Kashin-Beck Disease
Condition: Kashin-Beck Disease
Intervention: Dietary Supplement: Biological Antioxidant Supplementation
31 Enrolling by invitation A Multicenter, Multinational Clinical Assessment Study for Pediatric Patients With Achondroplasia
Condition: Achondroplasia
Intervention:
32 Active, not recruiting Trial of Lithium Carbonate for Treatment of Osteoporosis-pseudoglioma Syndrome
Condition: Osteoporosis Pseudoglioma
Intervention: Drug: Lithium
33 Terminated A Randomised Multi-centre Study to Compare the Long-term Performance of the Future Hip to 3 Other Implants in Primary Total Hip Replacement
Conditions: Osteoarthritis;   Post-traumatic Arthritis;   Collagen Disorders;   Avascular Necrosis;   Traumatic Femoral Fractures;   Nonunion of Femoral Fractures;   Congenital Hip Dysplasia;   Slipped Capital Femoral Epiphysis;   Perthes Disease
Interventions: Device: Future Hip;   Device: Omniflex;   Device: Zueymüller;   Device: CLS Spotorno
34 Terminated A Randomised Study to Compare Metal Ion Release and Long-term Performance of the Pinnacle™ Cup With a Ceramic-on-Metal or a Metal-on-Metal Bearing
Conditions: Osteoarthritis;   Post-traumatic Arthritis;   Collagen Disorders;   Avascular Necrosis;   Congenital Hip Dysplasia;   Slipped Capital Femoral Epiphysis
Intervention: Device: Pinnacle™ Acetabular System
35 Recruiting Mesenchymal Stem Cell Based Therapy for the Treatment of Osteogenesis Imperfecta
Condition: Osteogenesis Imperfecta
Intervention: Biological: Mesenchymal Stem Cells
36 Terminated rhPTH Therapy for Low Turnover Bone Fragility
Condition: Osteopetrosis
Intervention: Drug: rhPTH
37 Completed Efficacy and Safety of Alendronate in Chinese Children or Adolescents With Osteogenesis Imperfecta
Condition: Osteogenesis Imperfecta
Intervention: Drug: Alendronate
38 Terminated A Two Centre Study to Assess the Stability and Long-term Performance of the C-Stem™ AMT in a Total Primary Hip Replacement
Conditions: Rheumatoid Arthritis;   Osteoarthritis;   Post-traumatic Arthritis;   Collagen Disorders;   Avascular Necrosis;   Traumatic Femoral Fractures;   Nonunion of Femoral Fractures;   Congenital Hip Dysplasia;   Slipped Capital Femoral Epiphysis.
Intervention: Device: C-Stem™ AMT Femoral Component (standard and high off-set variants)
39 Completed Studies on Abnormal Bone From Patients With Polyostotic Fibrous Dysplasia and McCune Albright Syndrome
Condition: Polyostotic Fibrous Dysplasia
Intervention:
40 Active, not recruiting A Phase 2 Study of BMN 111 to Evaluate Safety, Tolerability, and Efficacy in Children With Achondroplasia
Condition: Achondroplasia
Intervention: Drug: BMN 111

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Indicates status has not been verified in more than two years