100 studies found for:    "mucopolysaccharidosis type IV"
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Rank Status Study
21 Active, not recruiting BMN 110 Phase 3B in Australian Patients
Condition: Mucopolysaccharidosis IVA (Morquio A Syndrome)
Intervention: Drug: BMN 110
22 Approved for marketing BMN 110 US Expanded Access Program
Conditions: Mucopolysaccharidosis IVA;   Morquio A Syndrome;   MPS IVA
Intervention: Drug: BMN 110
23 Active, not recruiting Study of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome)
Conditions: Mucopolysaccharidosis IVA;   Morquio A Syndrome;   MPS IVA
Intervention: Drug: BMN 110
24 Terminated Safety and Exercise Study of BMN 110 for Morquio A Syndrome
Conditions: Mucopolysaccharidosis IVA;   Morquio A Syndrome;   MPS IVA
Intervention: Drug: BMN 110
25 Terminated Establishing the Genetic Profile of Multiple Hereditary Exostoses (HME) in Families of BC
Condition: Exostoses, Multiple Hereditary
Intervention:
26 Unknown  Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells
Conditions: Sickle Cell Disease;   Thalassemia;   Anemia;   Granuloma;   Wiskott-Aldrich Syndrome;   Chediak Higashi Syndrome;   Osteopetrosis;   Neutropenia;   Thrombocytopenia;   Hurler Disease;   Niemann-Pick Disease;   Fucosidosis
Intervention: Procedure: Hematopoietic stem cell transplantation
27 Recruiting Screening and Natural History of Patients With Polyostotic Fibrous Dysplasia and McCune-Albright Syndrome
Condition: Polyostotic Fibrous Dysplasia
Intervention:
28 Completed A Study of the Effects of Pegvisomant on Growth Hormone Excess in McCune-Albright Syndrome
Conditions: McCune Albright Syndrome;   Polyostotic Fibrous Dysplasia
Intervention: Drug: Pegvisomant
29 Recruiting Evaluation of Skeletal Maturity for Slipped Capital Femoral Epiphysis
Condition: Slipped Capital Femoral Epiphysis
Intervention: Radiation: Radiographic skeletal age assessment
30 Terminated A Multi-centre Study to Assess the Long-term Performance of the DePuy ASR™ System in Primary Hip Resurfacing Surgery
Conditions: Rheumatoid Arthritis;   Osteoarthritis;   Post-traumatic Arthritis;   Collagen Disorders;   Avascular Necrosis;   Nonunion of Femoral Fractures;   Congenital Hip Dysplasia;   Slipped Capital Femoral Epiphysis.
Intervention: Device: DePuy ASR Hip System
31 Completed A Study to Evaluate Safety and Tolerability of BMN 111 Administered to Healthy Adult Volunteers
Condition: Achondroplasia
Interventions: Drug: BMN 111;   Drug: Normal Saline
32 Completed Bisphosphonate Therapy for Osteogenesis Imperfecta
Conditions: Osteogenesis Imperfecta;   Osteoporosis;   Paget Disease of Bone
Interventions: Drug: Alendronate;   Drug: Pamidronate
33 Completed Immune Response in the SAPHO Syndrome
Condition: SAPHO Syndrome
Intervention:
34 Recruiting The Effect of Treatment With Teriparatide and Zoledronic Acid in Patients With Osteogenesis Imperfecta
Condition: Osteogenesis Imperfecta
Interventions: Drug: Zoledronic acid;   Drug: Teriparatide;   Drug: placebo zoledronic acid;   Drug: placebo teriparatide
35 Completed Special Survey for Long Term Application
Conditions: Genetic Disorder;   Achondroplasia
Intervention: Drug: somatropin
36 Withdrawn A Multi-centre Study to Assess the Long-term Performance of the Pinnacle™ Cup With a Polyethylene-on-metal Bearing in Primary Total Hip Replacement
Conditions: Rheumatoid Arthritis;   Osteoarthritis;   Post-traumatic Arthritis;   Collagen Disorders;   Avascular Necrosis;   Traumatic Femoral Fractures;   Nonunion of Femoral Fractures;   Congenital Hip Dysplasia;   Slipped Capital Femoral Epiphysis.
Intervention: Device: Pinnacle Acetabular System
37 Enrolling by invitation A Survey Collecting Data on Adult Height in Patients With Achondroplasia Treated With Somatropin
Conditions: Genetic Disorder;   Achondroplasia
Intervention: Drug: somatropin
38 Completed Post Marketing Surveillance Study of Actimmune in Patients With Severe, Malignant Osteopetrosis
Condition: Osteopetrosis
Intervention: Drug: Actimmune Registry
39 Unknown  A Randomised Single Centre Study to Compare the Long-Term Wear Characteristics of Marathon™ and Enduron™ Polyethylene Cup Liners in Primary Total Hip Replacement
Conditions: Osteoarthritis;   Post-Traumatic Arthritis;   Collagen Disorders;   Avascular Necrosis;   Traumatic Femoral Fractures;   Nonunion of Femoral Fractures;   Congenital Hip Dysplasia;   Slipped Capital Femoral Epiphysis
Interventions: Device: Marathon™;   Device: Enduron
40 Unknown  TOCILIZUMAB IN FIBROUS DYSPLASIA OF BONE
Condition: Fibrous Dysplasia of Bone
Interventions: Drug: Tocilizumab;   Drug: Placebo

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Indicates status has not been verified in more than two years