103 studies found for:    "mucopolysaccharidosis type IV"
Show Display Options
Rank Status Study
21 Active, not recruiting BMN 110 Phase 3B in Australian Patients
Condition: Mucopolysaccharidosis IVA (Morquio A Syndrome)
Intervention: Drug: BMN 110
22 Approved for marketing BMN 110 US Expanded Access Program
Conditions: Mucopolysaccharidosis IVA;   Morquio A Syndrome;   MPS IVA
Intervention: Drug: BMN 110
23 Terminated Efficacy and Safety Study of BMN 110 for Morquio A Syndrome Patients Who Have Limited Ambulation
Conditions: Mucopolysaccharidosis IVA;   Morquio A Syndrome;   MPS IVA
Intervention: Drug: BMN 110
24 Terminated Safety and Exercise Study of BMN 110 for Morquio A Syndrome
Conditions: Mucopolysaccharidosis IVA;   Morquio A Syndrome;   MPS IVA
Intervention: Drug: BMN 110
25 Active, not recruiting Study of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome)
Conditions: Mucopolysaccharidosis IVA;   Morquio A Syndrome;   MPS IVA
Intervention: Drug: BMN 110
26 Not yet recruiting Urinary Biomarkers of OI Pathobiology
Condition: Osteogenesis Imperfecta
Intervention:
27 Recruiting Natural History, Pathogenesis and Outcome of Melorheostosis A Rare Osteosclerotic Disease
Condition: Rheumatic Disease
Intervention:
28 Recruiting BBD Longitudinal Study of Osteogenesis Imperfecta
Condition: Osteogenesis Imperfecta
Intervention:
29 Recruiting Multicenter,Single-arm Study to Evaluate Efficacy, Safety, & Pharmacokinetics of Denosumab in Children w/ OI
Condition: Osteogenesis Imperfecta
Intervention: Drug: Denosumab
30 Completed Efficacy and Safety of Alendronate in Chinese Children or Adolescents With Osteogenesis Imperfecta
Condition: Osteogenesis Imperfecta
Intervention: Drug: Alendronate
31 Recruiting Mesenchymal Stem Cell Based Therapy for the Treatment of Osteogenesis Imperfecta
Condition: Osteogenesis Imperfecta
Intervention: Biological: Mesenchymal Stem Cells
32 Recruiting MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
Conditions: Mucopolysaccharidosis I;   Mucopolysaccharidosis II;   Mucopolysaccharidosis VI;   Mucopolysaccharidosis VII;   Hurler Syndrome;   Hunter Syndrome;   Maroteaux Lamy Syndrome;   Sly Syndrome;   Glycoprotein Metabolic Disorders;   Alpha Mannosidosis;   Fucosidosis;   Aspartylglucosaminuria;   Adrenoleukodystrophy;   Peroxisomal Disorders;   Osteopetrosis;   Sphingolipidosis;   Gangliosidosis;   Globoid Cell Leukodystrophy;   Metachromatic Leukodystrophy;   Niemann Pick B;   Niemann Pick C Subtype 2;   I-cell Disease
Interventions: Procedure: blood stem cell transplant;   Drug: Rabbit Anti-Thymocyte Globulin (ATG);   Drug: Fludarabine;   Drug: Busulfan;   Drug: Cyclophosphamide;   Drug: Cyclosporine A (CSA);   Drug: Methylprednisolone;   Drug: Mycophenolate Mofetil (MMF);   Drug: Granulocyte-Colony Stimulating Factor (G-CSF);   Drug: Granulocyte-Macrophage Colony-Stimulating Factor (GM-CSF);   Drug: N-acetylcysteine;   Drug: Celecoxib;   Drug: Vitamin E;   Drug: Alpha Lipoic Acid
33 Active, not recruiting A Phase 2 Study of BMN 111 to Evaluate Safety, Tolerability, and Efficacy in Children With Achondroplasia
Condition: Achondroplasia
Intervention: Drug: BMN 111
34 Recruiting Natural History of Cherubism Observational Study
Condition: Cherubism
Intervention: Other: no interventions
35 Completed Translational Therapy in Patients With Osteogenesis Imperfecta - A Pilot Trial on Treatment With the Rankl-Antibody Denosumab
Condition: Osteogenesis Imperfecta
Intervention: Drug: Denosumab
36 Unknown  TOCILIZUMAB IN FIBROUS DYSPLASIA OF BONE
Condition: Fibrous Dysplasia of Bone
Interventions: Drug: Tocilizumab;   Drug: Placebo
37 Completed Effect of High-Dose Vitamin D on Bone Density in Osteogenesis Imperfecta
Condition: Osteogenesis Imperfecta
Interventions: Dietary Supplement: standard-dose vitamin D (400IU per day);   Dietary Supplement: high-dose vitamin D (2000 IU per day)
38 Completed Immune Response in the SAPHO Syndrome
Condition: SAPHO Syndrome
Intervention:
39 Recruiting The Effect of Treatment With Teriparatide and Zoledronic Acid in Patients With Osteogenesis Imperfecta
Condition: Osteogenesis Imperfecta
Interventions: Drug: Zoledronic acid;   Drug: Teriparatide;   Drug: placebo zoledronic acid;   Drug: placebo teriparatide
40 Recruiting Genetic and Functional Analysis of Cherubism
Condition: Cherubism
Intervention:

First Page    Show previous page of results Previous Page (1-20) Studies Shown (21-40) Next Page (41-60) Show next page of results    Last Page
Indicates status has not been verified in more than two years