A Natural History Study of Canavan Disease
GTA-Glyceryltriacetate for Canavan Disease
Oral Glyceryl Triacetate (GTA) in Newborns With Canavan
Lithium and Acetate for Canavan Disease
|5||Active, not recruiting||
Efficacy Study of an Online Educational Module Before Carrier Genetic Screening in Persons of Ashkenazi Jewish Descent.
ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases
† Study has passed its completion date and status has not been verified in more than two years.