11 studies found for:    "Spinal muscular atrophy 1"
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Study Details
Participant Details
Identifiers
Dates
Rank Status Study
1 Terminated
Has Results
Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Type I
Condition: Spinal Muscular Atrophy Type I
Intervention: Drug: sodium phenylbutyrate
2 Recruiting Pilot Study of an Innovative Physiotherapy in Patients With Infantile Spinal Muscular Atrophy (SMA)
Condition: Infantile Spinal Muscular Atrophy of Type 2 or 3
Intervention: Other: Physical exercise in a swimming pool during 6 months
3 Active, not recruiting Gene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1
Condition: Spinal Muscular Atrophy 1
Intervention: Biological: AVXS-101
4 Active, not recruiting Palliative Care in Spinal Muscular Atrophy (SMA) 1
Condition: Spinal Muscular Atrophy 1
Intervention: Other: Follow-up diary and questionnaire
5 Completed
Has Results
CARNIVAL Type I: Valproic Acid and Carnitine in Infants With Spinal Muscular Atrophy (SMA) Type I
Condition: Spinal Muscular Atrophy Type I
Intervention: Drug: Valproic Acid and Levocarnitine
6 Recruiting Allogeneic Adipose Derived Stem Cells for Werdnig Hoffman Patients
Condition: Infantile Spinal Muscular Atrophy, Type I [Werdnig- Hoffman]
Intervention: Biological: Adipose derived mesenchymal stem cell
7 Completed A Pilot Therapeutic Trial Using Hydroxyurea in Type I Spinal Muscular Atrophy Patients
Condition: Muscular Atrophy, Spinal
Intervention: Drug: Hydroxyurea
8 Terminated Infants With Spinal Muscular Atrophy Type I
Condition: Spinal Muscular Atrophy
Intervention:
9 Recruiting International SMA Patient Registry
Condition: Muscular Atrophy, Spinal
Intervention:
10 Recruiting Prospective Evaluation of Infants With Spinal Muscular Atrophy:
Condition: Spinal Muscular Atrophy
Intervention:
11 Completed A Pilot Study of Biomarkers for Spinal Muscular Atrophy
Condition: Spinal Muscular Atrophy
Intervention:

Indicates status has not been verified in more than two years