5 studies found for: "Pearson marrow-pancreas syndrome"
|1||Enrolling by invitation||
Natural History of Pearson Syndrome
Phase 2 Study of EPI-743 in Children With Pearson Syndrome
Assessing Immune Function in Young Patients With Cytopenia That Did Not Respond to Treatment
Effect of Bezafibrate on Muscle Metabolism in Patients With Fatty Acid Oxidation Defects
High Protein Diet in Patients With Long-chain Fatty Acid Oxidation Disorders
† Indicates status has not been verified in more than two years