7 studies found for: "Pearson marrow-pancreas syndrome"
|1||Enrolling by invitation||
Natural History of Pearson Syndrome
Phase 2 Study of EPI-743 in Children With Pearson Syndrome
Effect of Bezafibrate on Muscle Metabolism in Patients With Fatty Acid Oxidation Defects
Assessing Immune Function in Young Patients With Cytopenia That Did Not Respond to Treatment
High Protein Diet in Patients With Long-chain Fatty Acid Oxidation Disorders
Fatty Acid Oxidation Defects and Insulin Sensitivity
Fat and Sugar Metabolism During Exercise in Patients With Metabolic Myopathy
† Study has passed its completion date and status has not been verified in more than two years.