7 studies found for: "Pantothenate kinase-associated neurodegeneration"
|1||Active, not recruiting||
Long-term Deferiprone Treatment in Patients With Pantothenate Kinase-Associated Neurodegeneration
A Two-arm Efficacy and Safety Study of Deferiprone in Patients With Pantothenate Kinase-associated Neurodegeneration (PKAN)
Brain Perfusion in Pantothenate Kinase-associated Neurodegeneration (PKAN)
Compassionate Use of Deferiprone in Patients With PKAN
Efficacy and Safety Study of Fosmetpantotenate (RE-024) in PKAN Patients
NBIAready: Online Collection of Natural History Patient-reported Outcome Measures
|7||Active, not recruiting||
Ferrochelating Treatment in Patients Affected by Neurodegeneration With Brain Iron Accumulation (NBIA)
† Study has passed its completion date and status has not been verified in more than two years.