23 studies found for:    "Muscular Dystrophies, Limb-Girdle"
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Rank Status Study
1 Recruiting Limb Girdle Muscular Dystrophy (LGMD) Natural History
Condition: Muscular Dystrophies, Limb-Girdle (GENETICALLY CONFIRMED)
Intervention:
2 Completed Evaluation of Limb-Girdle Muscular Dystrophy
Conditions: Becker Muscular Dystrophy;   Limb-Girdle Muscular Dystrophy, Type 2A (Calpain-3 Deficiency);   Limb-Girdle Muscular Dystrophy, Type 2B (Miyoshi Myopathy, Dysferlin Deficiency);   Limb-Girdle Muscular Dystrophy, Type 2I (FKRP-deficiency)
Intervention:
3 Recruiting Cell Therapy in Limb Girdle Muscular Dystrophy
Condition: Limb Girdle Muscular Dystrophy
Intervention: Biological: Stem Cell
4 Completed Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C
Conditions: Limb Girdle Muscular Dystrophy Type 2C;   Gamma-sarcoglycanopathy
Intervention: Biological: AAV1-gamma-sarcoglycan vector injection
5 Completed Stem Cell Therapy in Limb Girdle Muscular Dystrophy
Condition: Limb Girdle Muscular Dystrophy
Intervention: Biological: Autologous bone marrow mononuclear cell transplantation
6 Active, not recruiting Genetic Characterization of Individuals With Limb Girdle Muscular Dystrophy
Condition: Limb-Girdle Muscular Dystrophy
Intervention:
7 Unknown  Muscle MRI in Becker Muscular Dystrophy and in Limb-girdle Muscular Dystrophy Type 2I
Conditions: Becker Muscular Dystrophy;   Limb-Girdle Muscular Dystrophy Type 2I
Intervention:
8 Enrolling by invitation Gene Transfer Clinical Trial for LGMD2D (Alpha-sarcoglycan Deficiency) Using scAAVrh74.tMCK.hSGCA
Condition: Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)
Intervention: Drug: scAAVrh74.tMCK.hSGCA
9 Completed Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)
Condition: Muscular Dystrophies
Interventions: Genetic: rAAV1.tMCK.human-alpha-sarcoglycan- First cohort;   Genetic: Genetic: rAAV1.tMCK.human-alpha-sarcoglycan- Second cohort
10 Enrolling by invitation Study to Evaluate the Long-Term Safety, Tolerability, and Biological Activity of ATYR1940 in Patients With Limb Girdle and Facioscapulohumeral Muscular Dystrophy
Conditions: Facioscapulohumeral Muscular Dystrophy;   Limb Girdle Muscular Dystrophy
Intervention: Drug: ATYR1940
11 Recruiting MRI on Persons With Mutations in POMT2 Gene (LGMD2N)
Condition: Limb-girdle Muscular Dystrophy
Intervention:
12 Completed MRI and Muscle Involvement in Patients With Mutations in GMPPB
Condition: Limb-girdle Muscular Dystrophy
Intervention:
13 Enrolling by invitation Clinical Trial of Coenzyme Q10 and Lisinopril in Muscular Dystrophies
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy;   Limb Girdle Muscular Dystrophy
Intervention: Drug: Coenzyme Q10 and Lisinopril
14 Completed Cardiac Magnetic Resonance in Children With Muscular Dystrophy
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy;   Limb Girdle Muscular Dystrophy
Intervention:
15 Completed Cardiac Outcome Measures in Children With Muscular Dystrophy
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy;   Limb Girdle Muscular Dystrophy
Intervention:
16 Completed
Has Results
Safety Study of Transvenous Limb Perfusion in Human Muscular Dystrophy
Conditions: Muscular Dystrophies;   Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy;   Limb-Girdle Muscular Dystrophy
Intervention: Other: Retrograde high pressure transvenous perfusion with normal saline
17 Unknown  Molecular Analysis of Patients With Neuromuscular Disease
Conditions: Limb-girdle Muscular Dystrophy;   Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy;   Facioscapulohumeral Muscular Dystrophy
Intervention:
18 Completed Study Evaluating MYO-029 in Adult Muscular Dystrophy
Conditions: Becker Muscular Dystrophy;   Facioscapulohumeral Muscular Dystrophy;   Limb-Girdle Muscular Dystrophy
Intervention: Drug: MYO-029
19 Recruiting The Safety and Biological Activity of ATYR1940 in Patients With Limb Girdle or Facioscapulohumeral Muscular Dystrophies
Conditions: Limb-Girdle Muscular Dystrophies;   Facioscapulohumeral Muscular Dystrophy
Interventions: Biological: ATYR1940;   Biological: Placebo
20 Recruiting rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies
Condition: Dysferlinopathy
Intervention: Drug: rAAVrh74.MHCK7.DYSF.DV

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Indicates status has not been verified in more than two years