6 studies found for: "Miyoshi myopathy" OR "Miyoshi muscular dystrophy" OR "anoctaminopathy" OR "dysferlinopathy"
|1||Active, not recruiting||
Clinical Outcome Study for Dysferlinopathy
Deflazacort in Dysferlinopathies
rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies
Proteasomal Inhibition for Patients With Mis-sense Mutated Dysferlin
Genetic Study of Familial and Sporadic ALS/Motor Neuron Disease, Miyoshi Myopathy and Other Neuromuscular Disorders
Evaluation of Limb-Girdle Muscular Dystrophy
† Study has passed its completion date and status has not been verified in more than two years.