11 studies found for: "Limb-girdle muscular dystrophy type 2A"
A Trial of PF-06252616 in Ambulatory Participants With LGMD2I
|2||Enrolling by invitation||
Gene Transfer Clinical Trial for LGMD2D (Alpha-sarcoglycan Deficiency) Using scAAVrh74.tMCK.hSGCA
Muscle MRI in Becker Muscular Dystrophy and in Limb-girdle Muscular Dystrophy Type 2I
Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C
Deflazacort in Dysferlinopathies
Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)
MRI on Persons With Mutations in POMT2 Gene (LGMD2N)
|8||Active, not recruiting||
Clinical Outcome Study for Dysferlinopathy
Congenital Muscle Disease Study of Patient and Family Reported Medical Information
The Safety and Biological Activity of ATYR1940 in Patients With Limb Girdle or Facioscapulohumeral Muscular Dystrophies
rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies
† Study has passed its completion date and status has not been verified in more than two years.