2 studies found for: "Leber congenital amaurosis type 2"
Active, not recruiting
Phase 1/2 Safety and Efficacy Study of AAV-RPE65 Vector to Treat Leber Congenital Amaurosis
Long-Term Follow-Up Gene Therapy Study for Leber Congenital Amaurosis OPTIRPE65 (Retinal Dystrophy Associated With Defects in RPE65)
† Study has passed its completion date and status has not been verified in more than two years.