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5 studies found for:    "Inherited bone marrow failure syndromes"
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Study Details
Participant Details
Identifiers
Dates
Rank Status Study
1 Recruiting Cancer in Inherited Bone Marrow Failure Syndromes
Conditions: Aplastic Anemia;   Head and Neck Neoplasms;   Bone Marrow Failure
Intervention:
2 Recruiting Unrelated And Partially Matched Related Donor PSCT w/ TCR αβ Depletion for Patients With BMF
Conditions: Acquired Aplastic Anemia;   Paroxysmal Nocturnal Hemoglobinuria;   Inherited Bone Marrow Failure Syndromes
Intervention: Device: CliniMACs
3 Completed Phase II Pilot Study of Granulocyte Colony-Stimulating Factor for Inherited Bone Marrow Failure Syndromes
Conditions: Shwachman Syndrome;   Fanconi's Anemia;   Dyskeratosis Congenita;   Thrombocytopenia
Intervention: Drug: filgrastim
4 Recruiting Pre-myeloid Cancer and Bone Marrow Failure Clinic Study
Conditions: Myeloid Malignancy;   Inherited Bone Marrow Failure Syndrome;   Clonal Expansion;   Cytopenia
Intervention: Other: follow up
5 Recruiting Safety Study of Gene Modified Donor T Cell Infusion After Stem Cell Transplant for Non-Malignant Diseases
Conditions: Primary Immune Deficiency Disorders;   Hemophagocytic Lymphohistiocytosis;   Inherited Bone Marrow Failure Syndrome;   Hemoglobinopathies;   Metabolic Disorders
Intervention: Biological: BPX-501 and AP1903

Study has passed its completion date and status has not been verified in more than two years.