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87 studies found for:    "Gaucher disease"
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Rank Status Study
1 Completed Cellular and Molecular Mechanisms Governing Bone Marrow Stem Cells in Gaucher Disease
Condition: Gaucher Disease
Intervention: Other: Bone marrow and blood sampling
2 Completed
Has Results
Open-Label Extension Study Evaluating Long Term Safety in Patients With Type 1 Gaucher Disease Receiving DRX008A (ERT)
Condition: Gaucher Disease
Intervention: Drug: GA-GCB
3 Completed
Has Results
A Multicenter Extension Study of Taliglucerase Alfa in Pediatric Subjects With Gaucher Disease
Condition: Gaucher Disease
Intervention: Drug: Taliglucerase alfa
4 Completed
Has Results
A Safety and Efficacy Study of Two Dose Levels of Taliglucerase Alfa in Pediatric Subjects With Gaucher Disease
Condition: Gaucher Disease
Intervention: Drug: Taliglucerase alfa
5 Recruiting Miglustat on Gaucher Disease Type IIIB
Condition: Gaucher Disease
Interventions: Drug: Miglustat;   Drug: ERT
6 Enrolling by invitation Identification of Undiagnosed Gaucher Disease
Condition: Gaucher Disease
Intervention: Other: Enzyme analysis
7 Unknown  Intra-monocyte Imiglucerase Kinetics in Gaucher Disease
Condition: Gaucher Disease
Intervention: Drug: Imiglucérase (drug) pharmacokinetics
8 Active, not recruiting Exploration of Immunity in Gaucher Disease
Condition: Gaucher Disease
Intervention:
9 Completed Validating a New Severity Score System for Adults With Type 1 Gaucher Disease (GD1)
Condition: Gaucher Disease
Intervention: Drug: Imiglucerase
10 Completed Bone Response to Enzyme Replacement in Gaucher's Disease
Condition: Gaucher's Disease
Intervention: Drug: CEREDASE™
11 Completed Study to Evaluate Blood Cell Lines From Patients With Gaucher Disease
Condition: Gaucher Disease
Intervention: Procedure: Blood sample
12 Completed Effects of Enzyme Replacement in Gaucher's Disease
Condition: Gaucher's Disease
Intervention:
13 Suspended Clinical Trial of Ambroxol in Patients With Type I Gaucher Disease
Condition: Type I Gaucher Disease
Intervention: Drug: Ambroxol
14 Recruiting Role of Oxidative Stress and Inflammation in Type 1 Gaucher Disease (GD1)
Condition: Gaucher Disease Type 1
Intervention: Drug: N-acetylcysteine
15 Completed PEG-Glucocerebrosidase for the Treatment of Gaucher Disease
Condition: Gaucher's Disease
Intervention: Drug: Lysodase
16 Completed A Study to Evaluate and Characterize the Effect of Pharmacological Chemicals on Blood From Patients With Gaucher Disease
Condition: Gaucher Disease
Intervention:
17 No longer available Expanded Access Trial of Plant Expressed Recombinant Glucocerebrosidase (prGCD) in Patients With Gaucher Disease
Condition: Gaucher Disease
Intervention: Drug: Plant cell expressed recombinant glucocerebrosidase (prGCD)
18 Completed OGT 918-006: A Phase I/II Randomized, Controlled Study of OGT 918 in Patients With Neuronopathic Gaucher Disease
Condition: Gaucher Disease
Intervention: Drug: OGT 918
19 Recruiting Home Therapy With VPRIV in Gaucher's Disease
Condition: Gaucher Disease
Intervention:
20 Completed
Has Results
A Study of Eliglustat Tartrate (Genz-112638) in Patients With Gaucher Disease to Evaluate Once Daily Versus Twice Daily Dosing (EDGE)
Condition: Gaucher Disease
Intervention: Drug: Eliglustat tartrate

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Study has passed its completion date and status has not been verified in more than two years.