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113 studies found for:    "Fabry disease"
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Rank Status Study
21 Recruiting Autologous Stem Cell Transplantation of Cells Engineered to Express Alpha-Galactosidase A in Patients With Fabry Disease
Condition: Fabry Disease
Intervention: Biological: Lentivirus Alpha-gal A transduced stem cells
22 Recruiting Fabry Disease in Cerebrovascular Disease
Condition: Fabry Disease
Intervention: Genetic: 26 common Fabry mutation types in Taiwan
23 Completed Alpha-Galactosidase A Replacement Therapy for Fabry Disease
Condition: Fabry Disease
Intervention: Drug: DRX005B
24 Completed Study to Collect Data on Fabry Disease Patients With Enhanceable Alpha-Galactosidase A Activity
Condition: Fabry Disease
Intervention:
25 Completed Neuropathic Pain and Fabry Disease
Condition: Fabry Disease
Intervention:
26 Completed An Open-Label Clinical Trial of Replagal Enzyme Therapy in Children Ages 7-17 Years With Fabry Disease
Condition: Fabry Disease
Intervention: Drug: Replagal
27 Completed
Has Results
Replagal Enzyme Replacement Therapy for Children With Fabry Disease
Condition: Fabry Disease
Intervention: Drug: Agalsidase alfa
28 Terminated Enzyme Replacement Therapy in Fabry Disease
Condition: Fabry Disease
Intervention: Other: Biochemical analyses.
29 Available Physician Initiated Expanded Access Request for Migalastat in Individual Patients With Fabry Disease
Condition: Fabry Disease
Intervention: Drug: migalastat HCl
30 Unknown  Pulmonary Disease and Exercise Tolerance in Boys With Fabry Disease
Condition: Fabry Disease
Intervention:
31 No longer available Treatment Protocol of Replagal for Patients With Fabry Disease
Condition: Fabry Disease
Intervention: Biological: agalsidase alfa
32 Completed Sophisticated Assessment of Disease Burden in Patients With Fabry Disease
Condition: Fabry Disease
Intervention: Procedure: MRI
33 Completed A Study of AT1001 in Patients With Fabry Disease
Condition: Fabry Disease
Intervention: Drug: AT1001 (migalastat hydrochloride)
34 Completed
Has Results
A Study of Fabrazyme in Pediatric Patients With Fabry Disease
Condition: Fabry Disease
Intervention: Biological: Fabrazyme (agalsidase beta)
35 Completed
Has Results
Safety Study of Replagal® Therapy in Children With Fabry Disease
Condition: Fabry Disease
Intervention: Biological: Replagal (agalsidase alfa)
36 Completed
Has Results
A Study of the Safety and Efficacy of Fabrazyme in Patients With Fabry Disease
Condition: Fabry Disease
Intervention: Biological: agalsidase beta
37 Completed A Study of the Safety and Efficacy of Fabrazyme in Patients With Fabry Disease
Condition: Fabry Disease
Intervention: Drug: Fabrazyme (agalsidase beta)
38 Completed A 12-Week Safety and Pharmacodynamic Study of AT1001 in Patients With Fabry Disease
Condition: Fabry Disease
Intervention: Drug: AT1001 (migalastat hydrochloride)
39 Completed A 24-Week Safety and Pharmacodynamic Study of AT1001 in Patients With Fabry Disease
Condition: Fabry Disease
Intervention: Drug: AT1001 (migalastat hydrochloride)
40 Enrolling by invitation Cardiac Involvement in Adult Patients With Fabry Disease; Relation to Enzyme Replacement Therapy
Condition: Fabry Disease
Intervention:

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Study has passed its completion date and status has not been verified in more than two years.