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4 studies found for:    "Dysferlinopathy"
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Rank Status Study
1 Completed Deflazacort in Dysferlinopathies
Conditions: LGMD2B;   Miyoshi Myopathy;   Dysferlinopathy
Interventions: Drug: deflazacort;   Drug: placebo
2 Active, not recruiting Clinical Outcome Study for Dysferlinopathy
Conditions: Dysferlinopathy;   LGMD2B;   Miyoshi Myopathy
3 Recruiting rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies
Condition: Dysferlinopathy
Intervention: Drug: rAAVrh74.MHCK7.DYSF.DV
4 Recruiting Proteasomal Inhibition for Patients With Mis-sense Mutated Dysferlin
Condition: Dysferlinopathy
Intervention: Drug: Bortezomib

Indicates status has not been verified in more than two years