Study of Metabolic Modifications in Children With Noonan Syndrome
Novel Treatment for Syndromic Ichthyoses
Combination Chemotherapy in Treating Young Patients With Down Syndrome and Acute Myeloid Leukemia or Myelodysplastic Syndromes
|4||Not yet recruiting||
Treatment of Steroid Dependent Idiopathic Nephrotic Syndrome in Children With Low Doses of Interleukin 2: a Pilot Study
Study of Inborn Errors of Cholesterol Synthesis and Related Disorders
† Study has passed its completion date and status has not been verified in more than two years.