Study of Metabolic Modifications in Children With Noonan Syndrome
Novel Treatment for Syndromic Ichthyoses
Active, not recruiting
Combination Chemotherapy in Treating Young Patients With Down Syndrome and Acute Myeloid Leukemia or Myelodysplastic Syndromes
Study of Inborn Errors of Cholesterol Synthesis and Related Disorders
† Study has passed its completion date and status has not been verified in more than two years.